Crigler-Najjar Syndrome Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update

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Crigler-Najjar syndrome is a severe condition characterized by high levels of a toxic substance called bilirubin in the blood. Symptoms include yellow skin and yellow in the whites of the eyes. It occurs when the enzyme that normally converts bilirubin into a form that can easily be removed from the body does not work correctly. Treatment includes phototherapy, liver transplantation, and blood transfusions.

The Crigler-Najjar Syndrome Drugs in Development market research report provides an overview of the Crigler-Najjar Syndrome pipeline landscape. The report provides comprehensive information on the therapeutics under development for Crigler-Najjar Syndrome, complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The report also covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases. Additionally, the report provides an overview of key players involved in therapeutic development for Crigler-Najjar Syndrome and features dormant and discontinued projects.

Crigler-Najjar Syndrome Pipeline Drugs Market Targets

The target of the Crigler-Najjar Syndrome pipeline drugs market is UDP Glucuronosyltransferase 1-1.

Mechanisms of Action of Crigler-Najjar Syndrome Pipeline Drugs Market

The mechanism of action of the Crigler-Najjar Syndrome pipeline drugs market is UDP Glucuronosyltransferase 1-1 Activator.

Routes of Administration in Crigler-Najjar Syndrome Pipeline Drugs Market

The routes of administration in the Crigler-Najjar Syndrome pipeline drugs market are intravenous and parenteral.

Crigler-Najjar Syndrome pipeline drugs market, by routes of administration

Crigler-Najjar Syndrome pipeline drugs market, by routes of administration

For more routes of administration insights, download a free report sample

Key Crigler-Najjar Syndrome Pipeline Drugs Market Companies

Some of the key companies in the Crigler-Najjar Syndrome pipeline drugs market are International Stem Cell Corp, Logicbio Therapeutics Inc, Moderna Inc, Selecta Bioscience Inc, and Promethera Biosciences SA.

Crigler-Najjar Syndrome pipeline drugs market, by key companies

Crigler-Najjar Syndrome pipeline drugs market, by key companies

To know more about key companies, download a free report sample

Market report overview

Target UDP Glucuronosyltransferase 1-1
Mechanism of Action UDP Glucuronosyltransferase 1-1 Activator
Routes of Administration Intravenous and Parenteral
Molecule Types Cell Therapy, Gene Therapy, and Oligonucleotide
Key Companies International Stem Cell Corp, Logicbio Therapeutics Inc, Moderna Inc, Selecta Bioscience Inc, and Promethera Biosciences SA

Scope

This report provides:

  • A snapshot of the global therapeutic landscape of Crigler-Najjar Syndrome (Genetic Disorders).
  • Reviews of pipeline therapeutics for Crigler-Najjar Syndrome (Genetic Disorders) by companies and universities/research institutes based on information derived from company and industry-specific sources.
  • Pipeline products based on several stages of development ranging from pre-registration to discovery and undisclosed stages.
  • Descriptive drug profiles for the pipeline products which include product description, descriptive MoA, R&D brief, licensing and collaboration details & other developmental activities.
  • Reviews of key companies involved in Crigler-Najjar Syndrome (Genetic Disorders) therapeutics and enlists all their major and minor projects.
  • Evaluation of Crigler-Najjar Syndrome (Genetic Disorders) targeted therapeutics based on drug target, mechanism of action (MoA), route of administration (RoA), and molecule type.
  • All the dormant and discontinued pipeline projects.
  • Reviews of the latest news and deals related to pipeline therapeutics for Crigler-Najjar Syndrome (Genetic Disorders).

Reasons to Buy

  • Procure strategically important competitor information, analysis, and insights to formulate effective R&D strategies.
  • Recognize emerging players with potentially strong product portfolio and create effective counter-strategies to gain competitive advantage.
  • Find and recognize significant and varied types of therapeutics under development for Crigler-Najjar Syndrome (Genetic Disorders).
  • Classify potential new clients or partners in the target demographic.
  • Develop tactical initiatives by understanding the focus areas of leading companies.
  • Plan mergers and acquisitions meritoriously by identifying key players and it’s most promising pipeline therapeutics.
  • Formulate corrective measures for pipeline projects by understanding Crigler-Najjar Syndrome (Genetic Disorders) pipeline depth and focus of Indication therapeutics.
  • Develop and design in-licensing and out-licensing strategies by identifying prospective partners with the most attractive projects to enhance and expand business potential and scope.
  • Adjust the therapeutic portfolio by recognizing discontinued projects and understand from the know-how what drove them from pipeline.

International Stem Cell Corp
Logicbio Therapeutics Inc
Moderna Inc
Promethera Biosciences SA

Table of Contents

Table of Contents

List of Tables

List of Figures

Introduction

Global Markets Direct Report Coverage

Crigler-Najjar Syndrome – Overview

Crigler-Najjar Syndrome – Therapeutics Development

Pipeline Overview

Pipeline by Companies

Pipeline by Universities/Institutes

Products under Development by Companies

Products under Development by Universities/Institutes

Crigler-Najjar Syndrome – Therapeutics Assessment

Assessment by Target

Assessment by Mechanism of Action

Assessment by Route of Administration

Assessment by Molecule Type

Crigler-Najjar Syndrome – Companies Involved in Therapeutics Development

International Stem Cell Corp

Logicbio Therapeutics Inc

Moderna Inc

Promethera Biosciences SA

Crigler-Najjar Syndrome – Drug Profiles

GNT-0003 – Drug Profile

Product Description

Mechanism Of Action

History of Events

HepaStem – Drug Profile

Product Description

Mechanism Of Action

History of Events

LB-301 – Drug Profile

Product Description

Mechanism Of Action

History of Events

mRNA-3351 – Drug Profile

Product Description

Mechanism Of Action

History of Events

Stem Cell Therapy for Alpha-Antitrypsin Deficiency, Crigler-Najjar Syndrome and Liver Cirrhosis – Drug Profile

Product Description

Mechanism Of Action

History of Events

Crigler-Najjar Syndrome – Dormant Projects

Crigler-Najjar Syndrome – Product Development Milestones

Featured News & Press Releases

May 04, 2021: LogicBio announces presentations at upcoming American Society of Gene and Cell Therapy (ASGCT) Annual Meeting

Feb 12, 2013: International Stem Cell Demonstrates Positive Animal Efficacy Results In Metabolic Liver Disease Program

Jan 07, 2013: International Stem Cell Announces Positive Animal Efficacy Results In Liver Disease Program

Appendix

Methodology

Coverage

Secondary Research

Primary Research

Expert Panel Validation

Contact Us

Disclaimer

Table

List of Tables

Number of Products under Development for Crigler-Najjar Syndrome, 2022

Number of Products under Development by Companies, 2022

Number of Products under Development by Universities/Institutes, 2022

Products under Development by Companies, 2022

Products under Development by Universities/Institutes, 2022

Number of Products by Stage and Target, 2022

Number of Products by Stage and Mechanism of Action, 2022

Number of Products by Stage and Route of Administration, 2022

Number of Products by Stage and Molecule Type, 2022

Crigler-Najjar Syndrome – Pipeline by International Stem Cell Corp, 2022

Crigler-Najjar Syndrome – Pipeline by Logicbio Therapeutics Inc, 2022

Crigler-Najjar Syndrome – Pipeline by Moderna Inc, 2022

Crigler-Najjar Syndrome – Pipeline by Promethera Biosciences SA, 2022

Crigler-Najjar Syndrome – Dormant Projects, 2022

Figures

List of Figures

Number of Products under Development for Crigler-Najjar Syndrome, 2022

Number of Products under Development by Companies, 2022

Number of Products by Stage and Targets, 2022

Number of Products by Stage and Mechanism of Actions, 2022

Number of Products by Routes of Administration, 2022

Number of Products by Stage and Routes of Administration, 2022

Number of Products by Molecule Types, 2022

Number of Products by Stage and Molecule Types, 2022

Frequently asked questions

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