Gorlin Syndrome (Basal Cell Nevus Syndrome/ Nevoid Basal Cell Carcinoma Syndrome) Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update

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Gorlin syndrome, also known as nevoid basal cell carcinoma syndrome, is a condition that affects many areas of the body  and  increases  the  risk  of  developing  various  cancerous  and noncancerous  tumors.  Symptoms  include arrhythmia,  medulloblastoma,  ovarian  fibromas,  depressions  in  the  skin,  large  head  size  and  skeletal  abnormalities involving the spine, ribs, or skull.

The Gorlin Syndrome – Drugs In Development research report provides a comprehensive overview on the therapeutics under development for Gorlin Syndrome, complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type.  The report also covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases.  Additionally, the report provides an overview of key players involved in therapeutic development for Gorlin Syndrome and features dormant and discontinued projects.

Key Targets in the Gorlin Syndrome Pipeline Drugs Market

The key targets in the Gorlin Syndrome pipeline drugs market are Smoothened Homolog, Serine/Threonine Protein Kinase mTOR, Lanosterol 14 Alpha Demethylase, and Programmed Cell Death Protein 1.

Gorlin Syndrome Pipeline Drugs Market, by Targets

Gorlin Syndrome Pipeline Drugs Market, by Targets

For more target insights, download a free report sample

Key MoA in the Gorlin Syndrome Pipeline Drugs Market

The key mechanisms of action in the Gorlin Syndrome pipeline drugs market are Smoothened Homolog Antagonist, Serine/Threonine Protein Kinase mTOR Inhibitor, Lanosterol 14 Alpha Demethylase Inhibitor, and Programmed Cell Death Protein 1 Antagonist.

Gorlin Syndrome Pipeline Drugs Market, by MoA

Gorlin Syndrome Pipeline Drugs Market, by MoA

To get more insights on key MoA, download a free sample report

Gorlin Syndrome Pipeline Drugs Market Segmentation by RoA

The key routes of administration in the Gorlin Syndrome pipeline drugs market are Intratumour, Intravenous, Oral, Topical, Intravenous Drip, Intralesional, and Intrathecal.

Gorlin Syndrome Pipeline Drugs Market Analysis, by RoA

Gorlin Syndrome Pipeline Drugs Market Analysis, by RoA

To get more insights on key RoA, download a free sample report

Key Molecule Types in the Gorlin Syndrome Pipeline Drugs Market

The key molecule types in the Gorlin Syndrome pipeline drugs market are Monoclonal Antibody, Small Molecule, and Protein among others.

Gorlin Syndrome Pipeline Drugs Market, by Molecule Type

Gorlin Syndrome Pipeline Drugs Market, by Molecule Type

To get more insights on key molecule types, download a free sample report

Major Companies in the Gorlin Syndrome Pipeline Drugs Market

The major companies in the Gorlin Syndrome pipeline drugs market are Kintara  Therapeutics  Inc, Genentech USA Inc, Feldan Therapeutics Inc, Mayne Pharma Group Ltd, Ono  Pharmaceutical  Co  Ltd, Palvella  Therapeutics  LLC  among others.

Gorlin Syndrome Pipeline Drugs Market, by Major Companies

Gorlin Syndrome Pipeline Drugs Market, by Major Companies

For more company insights, download a free sample report

Gorlin Syndrome Pipeline Drugs Market Overview

Key Targets Smoothened Homolog, Serine/Threonine Protein Kinase mTOR, Lanosterol 14 Alpha Demethylase, and Programmed Cell Death Protein 1
Key Mechanisms of action Smoothened Homolog Antagonist, Serine/Threonine Protein Kinase mTOR Inhibitor, Lanosterol 14 Alpha Demethylase Inhibitor, and Programmed Cell Death Protein 1 Antagonist
Key Routes of Administration Intratumour, Intravenous, Oral, Topical, Intravenous Drip, Intralesional, and Intrathecal
Key molecule types Monoclonal Antibody, Small Molecule, and Protein
Major companies Kintara  Therapeutics  Inc, Genentech USA Inc, Feldan Therapeutics Inc, Mayne Pharma Group Ltd, Ono  Pharmaceutical  Co  Ltd, Palvella  Therapeutics  LLC  and Others

Scope

  • The pipeline guide provides a snapshot of the global therapeutic landscape of Gorlin Syndrome
  • The pipeline guide reviews pipeline therapeutics for Gorlin Syndrome by companies and universities/research institutes based on information derived from company and industry-specific sources.
  • The pipeline guide covers pipeline products based on several stages of development ranging from pre-registration till discovery and undisclosed stages.
  • The pipeline guide features descriptive drug profiles for the pipeline products which comprise, product description, descriptive licensing and collaboration details, R&D brief, MoA & other developmental activities.
  • The pipeline guide reviews key companies involved in Gorlin Syndrome therapeutics and enlists all their major and minor projects.
  • The pipeline guide evaluates Gorlin Syndrome therapeutics based on mechanism of action (MoA), drug target, route of administration (RoA), and molecule type.
  • The pipeline guide encapsulates all the dormant and discontinued pipeline projects.
  • The pipeline guide reviews the latest news related to pipeline therapeutics for Gorlin Syndrome

Reasons to Buy

  • Procure strategically important competitor information, analysis, and insights to formulate effective R&D strategies.
  • Recognize emerging players with a potentially strong product portfolio and create effective counter-strategies to gain a competitive advantage.
  • Find and recognize significant and varied types of therapeutics under development for Gorlin Syndrome
  • Classify potential new clients or partners in the target demographic.
  • Develop tactical initiatives by understanding the focus areas of leading companies.
  • Plan mergers and acquisitions meritoriously by identifying key players and their most promising pipeline therapeutics.
  • Formulate corrective measures for pipeline projects by understanding Gorlin Syndrome pipeline depth and focus of Indication therapeutics.
  • Develop and design in-licensing and out-licensing strategies by identifying prospective partners with the most attractive projects to enhance and expand business potential and scope.
  • Adjust the therapeutic portfolio by recognizing discontinued projects and understand from the know-how what drove them from the pipeline.

Feldan Therapeutics Inc
Genentech USA Inc
Kintara Therapeutics Inc
Mayne Pharma Group Ltd
Ono Pharmaceutical Co Ltd
Palvella Therapeutics LLC
PellePharm Inc

Table of Contents

Table of Contents

List of Tables

List of Figures

Introduction

Global Markets Direct Report Coverage

Gorlin Syndrome (Basal Cell Nevus Syndrome/ Nevoid Basal Cell Carcinoma Syndrome) – Overview

Gorlin Syndrome (Basal Cell Nevus Syndrome/ Nevoid Basal Cell Carcinoma Syndrome) – Therapeutics Development

Pipeline Overview

Pipeline by Companies

Products under Development by Companies

Gorlin Syndrome (Basal Cell Nevus Syndrome/ Nevoid Basal Cell Carcinoma Syndrome) – Therapeutics Assessment

Assessment by Target

Assessment by Mechanism of Action

Assessment by Route of Administration

Assessment by Molecule Type

Gorlin Syndrome (Basal Cell Nevus Syndrome/ Nevoid Basal Cell Carcinoma Syndrome) – Companies Involved in Therapeutics Development

Feldan Therapeutics Inc

Genentech USA Inc

Kintara Therapeutics Inc

Mayne Pharma Group Ltd

Ono Pharmaceutical Co Ltd

Palvella Therapeutics LLC

PellePharm Inc

Gorlin Syndrome (Basal Cell Nevus Syndrome/ Nevoid Basal Cell Carcinoma Syndrome) – Drug Profiles

FTX-001 – Drug Profile

Product Description

Mechanism Of Action

itraconazole – Drug Profile

Product Description

Mechanism Of Action

History of Events

nivolumab – Drug Profile

Product Description

Mechanism Of Action

History of Events

patidegib hydrochloride – Drug Profile

Product Description

Mechanism Of Action

History of Events

PTX-367 – Drug Profile

Product Description

Mechanism Of Action

rostaporfin – Drug Profile

Product Description

Mechanism Of Action

History of Events

sirolimus – Drug Profile

Product Description

Mechanism Of Action

History of Events

vismodegib – Drug Profile

Product Description

Mechanism Of Action

History of Events

Gorlin Syndrome (Basal Cell Nevus Syndrome/ Nevoid Basal Cell Carcinoma Syndrome) – Dormant Projects

Gorlin Syndrome (Basal Cell Nevus Syndrome/ Nevoid Basal Cell Carcinoma Syndrome) – Discontinued Products

Gorlin Syndrome (Basal Cell Nevus Syndrome/ Nevoid Basal Cell Carcinoma Syndrome) – Product Development Milestones

Featured News & Press Releases

Oct 29, 2020: PellePharm to highlight clinical programs at the 29th congress of the European Academy of Dermatology and Venereology

Jan 08, 2020: PellePharm initiates phase 2 clinical trial of Patidegib topical gel for people with high frequency basal cell carcinoma

Dec 02, 2019: PellePharm completes enrollment of pivotal phase 3 clinical trial of Patidegib Topical Gel in patients with Gorlin Syndrome

Apr 01, 2019: PellePharm initiates pivotal phase 3 clinical trial of Patidegib topical gel in patients with gorlin syndrome

Dec 18, 2018: Mayne Pharma announces US commercial rights for Suba-itraconazole in BCCNS

Oct 15, 2018: Pellepharm presents updated data from two phase 2 studies demonstrating the potential of Patidegib topical gel to treat basal cell carcinomas in patients with gorlin syndrome and in patients with non-gorlin sporadic bccs

Oct 11, 2018: HedgePath Pharmaceuticals to present at the 2018 BioFlorida Annual Conference

Oct 09, 2018: HedgePath Pharmaceuticals pathway for filing SUBA BCCNS NDA clarified in Meeting with FDA

Jun 05, 2018: HedgePath Pharmaceuticals Granted Meeting with FDA to Discuss SUBA BCCNS Trial Data and Regulatory Pathway

May 16, 2018: PellePharm to present topical Patidegib and skin cancer epidemiological data at the 7th International Investigative Dermatology Meeting

Feb 22, 2018: Adgero Biopharmaceuticals Granted FDA Orphan Drug Designation of REM-001 Therapy for the Treatment of Basal Cell Carcinoma Nevus Syndrome

Jan 11, 2018: HedgePath Pharmaceuticals Receives Orphan Drug Designation for SUBA-Itraconazole from the European Medicines Agency

Nov 20, 2017: FDA Grants Breakthrough Therapy Designation and Orphan Drug Designation to Pellepharm for Topical Patidegib in Gorlin Syndrome

Oct 30, 2017: HedgePath Pharmaceuticals Completes Enrollment for its Phase 2(b) Trial in BCCNS and Provides Trial Update

Jul 31, 2017: PellePharm Announces Topline Results from Phase 2 Study of Topical Patidegib in Gorlin Syndrome Basal Cell Carcinomas

Appendix

Methodology

Coverage

Secondary Research

Primary Research

Expert Panel Validation

Contact Us

Disclaimer

Table

List of Tables

Number of Products under Development for Gorlin Syndrome (Basal Cell Nevus Syndrome/ Nevoid Basal Cell Carcinoma Syndrome), 2022

Number of Products under Development by Companies, 2022

Products under Development by Companies, 2022

Number of Products by Stage and Target, 2022

Number of Products by Stage and Mechanism of Action, 2022

Number of Products by Stage and Route of Administration, 2022

Number of Products by Stage and Molecule Type, 2022

Gorlin Syndrome (Basal Cell Nevus Syndrome/ Nevoid Basal Cell Carcinoma Syndrome) – Pipeline by Feldan Therapeutics Inc, 2022

Gorlin Syndrome (Basal Cell Nevus Syndrome/ Nevoid Basal Cell Carcinoma Syndrome) – Pipeline by Genentech USA Inc, 2022

Gorlin Syndrome (Basal Cell Nevus Syndrome/ Nevoid Basal Cell Carcinoma Syndrome) – Pipeline by Kintara Therapeutics Inc, 2022

Gorlin Syndrome (Basal Cell Nevus Syndrome/ Nevoid Basal Cell Carcinoma Syndrome) – Pipeline by Mayne Pharma Group Ltd, 2022

Gorlin Syndrome (Basal Cell Nevus Syndrome/ Nevoid Basal Cell Carcinoma Syndrome) – Pipeline by Ono Pharmaceutical Co Ltd, 2022

Gorlin Syndrome (Basal Cell Nevus Syndrome/ Nevoid Basal Cell Carcinoma Syndrome) – Pipeline by Palvella Therapeutics LLC, 2022

Gorlin Syndrome (Basal Cell Nevus Syndrome/ Nevoid Basal Cell Carcinoma Syndrome) – Pipeline by PellePharm Inc, 2022

Gorlin Syndrome (Basal Cell Nevus Syndrome/ Nevoid Basal Cell Carcinoma Syndrome) – Dormant Projects, 2022

Gorlin Syndrome (Basal Cell Nevus Syndrome/ Nevoid Basal Cell Carcinoma Syndrome) – Discontinued Products, 2022

Figures

List of Figures

Number of Products under Development for Gorlin Syndrome (Basal Cell Nevus Syndrome/ Nevoid Basal Cell Carcinoma Syndrome), 2022

Number of Products under Development by Companies, 2022

Number of Products by Targets, 2022

Number of Products by Stage and Targets, 2022

Number of Products by Mechanism of Actions, 2022

Number of Products by Stage and Mechanism of Actions, 2022

Number of Products by Routes of Administration, 2022

Number of Products by Stage and Routes of Administration, 2022

Number of Products by Molecule Types, 2022

Number of Products by Stage and Molecule Types, 2022

Frequently asked questions

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