Hemophilia B (Factor IX Deficiency) Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update

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Hemophilia B is a hereditary bleeding disorder caused by a lack of blood clotting factor IX. Its treatment includes replacing the defective clotting factor.

The Hemophilia B pipeline market research report provides comprehensive information on the therapeutics under development for Hemophilia B, complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA), and molecule type. The report also covers the descriptive pharmacological action of the therapeutics, its complete research and development history, and the latest news and press releases. Additionally, the report provides an overview of key players involved in therapeutic development for Hemophilia Band features dormant and discontinued projects.

Key Targets in the Hemophilia B Pipeline Products Market

The key targets in the Hemophilia B Pipeline products market are Coagulation Factor IX, Coagulation Factor VII, Tissue Factor Pathway Inhibitor, Coagulation Factor X, Antithrombin III, and Vitamin K Dependent Protein C.

Hemophilia B Pipeline Products Market Analysis by Targets

Hemophilia B Pipeline Products Market Analysis by Targets

For more target insights, download a free report sample

Key Mechanisms of Action in the Hemophilia B Pipeline Products Market

The key mechanisms of action in the Hemophilia B pipeline products market are Coagulation Factor IX Activator, Coagulation Factor IX Replacement, Coagulation Factor VII Replacement, Tissue Factor Pathway Inhibitor Inhibitor, Coagulation Factor X Activator, Antithrombin III Inhibitor, and Vitamin K Dependent Protein C Inhibitor.

Hemophilia B Pipeline Products Market Analysis by Mechanisms of Action

Hemophilia B Pipeline Products Market Analysis by Mechanisms of Action

For more mechanisms of action insights, download a free report sample

Key Routes of Administration in the Hemophilia B Pipeline Products Market

The key routes of administration in the Hemophilia B pipeline products market are intravenous, subcutaneous, parenteral, and intravenous bolus.

Hemophilia B Pipeline Products Market Analysis by Routes of Administration

Hemophilia B Pipeline Products Market Analysis by Routes of Administration

For more routes of administration insights, download a free report sample

Key Molecule Types in the Hemophilia B Pipeline Products Market

The key molecule types in the Hemophilia B pipeline products market are gene therapy, recombinant protein, gene-modified cell therapy, monoclonal antibody, fusion protein, protein, recombinant enzyme, antibody, and antisense RNAi oligonucleotide.

Hemophilia B Pipeline Products Market Analysis by Molecule Types

Hemophilia B Pipeline Products Market Analysis by Molecule Types

For more molecule type insights, download a free report sample

Major Companies in the Hemophilia B Pipeline Products Market

Some of the major companies in the Hemophilia B pipeline products market are OPKO Health Inc, Pfizer Inc, Catalyst Biosciences Inc, Freeline Therapeutics Holdings Plc, LFB SA, Novo Nordisk AS, Sanofi, SK Plasma Co Ltd, AlphaMab Co Ltd, and Amarna Therapeutics BV.

Hemophilia B Pipeline Products Market Analysis by Companies

Hemophilia B Pipeline Products Market Analysis by Companies

To know more about major companies, download a free report sample

Hemophilia B Pipeline Products Market Report Overview

Key Targets Coagulation Factor IX, Coagulation Factor VII, Tissue Factor Pathway Inhibitor, Coagulation Factor X, Antithrombin III, and Vitamin K Dependent Protein C
Key Mechanisms of Action Coagulation Factor IX Activator, Coagulation Factor IX Replacement, Coagulation Factor VII Replacement, Tissue Factor Pathway Inhibitor Inhibitor, Coagulation Factor X Activator, Antithrombin III Inhibitor, and Vitamin K Dependent Protein C Inhibitor
Key Routes of Administration Intravenous, Subcutaneous, Parenteral, and Intravenous Bolus
Key Molecule Type Gene Therapy, Recombinant Protein, Gene-Modified Cell Therapy, Monoclonal Antibody, Fusion Protein, Protein, Recombinant Enzyme, Antibody, and Antisense RNAi Oligonucleotide
Major Companies OPKO Health Inc, Pfizer Inc, Catalyst Biosciences Inc, Freeline Therapeutics Holdings Plc, LFB SA, Novo Nordisk AS, Sanofi, SK Plasma Co Ltd, AlphaMab Co Ltd, and Amarna Therapeutics B

Scope

  • The pipeline guide provides a snapshot of the global therapeutic landscape of Hemophilia B (Hematological Disorders).
  • The pipeline guide reviews pipeline therapeutics for Hemophilia B (Hematological Disorders) by companies and universities/research institutes based on information derived from company and industry-specific sources.
  • The pipeline guide covers pipeline products based on several stages of development ranging from pre-registration till discovery and undisclosed stages.
  • The pipeline guide features descriptive drug profiles for the pipeline products which comprise, product description, descriptive licensing and collaboration details, R&D brief, MoA & other developmental activities.
  • The pipeline guide reviews key companies involved in Hemophilia B (Hematological Disorders) therapeutics and enlists all their major and minor projects.
  • The pipeline guide evaluates Hemophilia B (Hematological Disorders) therapeutics based on mechanism of action (MoA), drug target, route of administration (RoA), and molecule type.
  • The pipeline guide encapsulates all the dormant and discontinued pipeline projects.
  • The pipeline guide reviews the latest news related to pipeline therapeutics for Hemophilia B (Hematological Disorders)

Reasons to Buy

  • Procure strategically important competitor information, analysis, and insights to formulate effective R&D strategies.
  • Recognize emerging players with potentially strong product portfolios and create effective counter-strategies to gain competitive advantage.
  • Find and recognize significant and varied types of therapeutics under development for Hemophilia B (Hematological Disorders).
  • Classify potential new clients or partners in the target demographic.
  • Develop tactical initiatives by understanding the focus areas of leading companies.
  • Plan mergers and acquisitions meritoriously by identifying key players and their most promising pipeline therapeutics.
  • Formulate corrective measures for pipeline projects by understanding Hemophilia B (Hematological Disorders) pipeline depth and focus of Indication therapeutics.
  • Develop and design in-licensing and out-licensing strategies by identifying prospective partners with the most attractive projects to enhance and expand business potential and scope.
  • Adjust the therapeutic portfolio by recognizing discontinued projects and understand from the know-how what drove them from the pipeline.

AlphaMab Co Ltd
Amarna Therapeutics BV
ASC Therapeutics Inc
Belief Biomed Inc
Biocad
Catalyst Biosciences Inc
Centessa Pharmaceuticals Plc
Chameleon Biosciences Inc
Chengdu Rongsheng Pharmaceutical Co Ltd
Chia Tai Tianqing Pharmaceutical Group Co Ltd
CSL Ltd
Daiichi Sankyo Co Ltd
Expression Therapeutics Inc
Freeline Therapeutics Holdings Plc
GC Pharma
GeneLeap Biotech
GeneVentiv Therapeutics Inc
Intellia Therapeutics Inc
LFB SA
Logicbio Therapeutics Inc
Novo Nordisk AS
OPKO Health Inc
Pfizer Inc
RegenxBio Inc
Sanofi
Sigilon Therapeutics Inc
SK Plasma Co Ltd
Staidson BioPharma Inc
ToolGen Inc
UBI Pharma Inc
UniQure NV
Zhengzhou Gensciences Inc

Table of Contents

Table of Contents

List of Tables

List of Figures

Introduction

Global Markets Direct Report Coverage

Hemophilia B (Factor IX Deficiency) – Overview

Hemophilia B (Factor IX Deficiency) – Therapeutics Development

Pipeline Overview

Pipeline by Companies

Pipeline by Universities/Institutes

Products under Development by Companies

Products under Development by Universities/Institutes

Hemophilia B (Factor IX Deficiency) – Therapeutics Assessment

Assessment by Target

Assessment by Mechanism of Action

Assessment by Route of Administration

Assessment by Molecule Type

Hemophilia B (Factor IX Deficiency) – Companies Involved in Therapeutics Development

Hemophilia B (Factor IX Deficiency) – Drug Profiles

Hemophilia B (Factor IX Deficiency) – Dormant Projects

Hemophilia B (Factor IX Deficiency) – Discontinued Products

Hemophilia B (Factor IX Deficiency) – Product Development Milestones

Featured News & Press Releases

Appendix

Methodology

Coverage

Secondary Research

Primary Research

Expert Panel Validation

Contact Us

Disclaimer

Table

List of Tables

Number of Products under Development for Hemophilia B (Factor IX Deficiency), 2022

Number of Products under Development by Companies, 2022

Number of Products under Development by Companies, 2022 (Contd..1)

Number of Products under Development by Universities/Institutes, 2022

Products under Development by Companies, 2022

Products under Development by Companies, 2022 (Contd..1)

Products under Development by Companies, 2022 (Contd..2)

Products under Development by Universities/Institutes, 2022

Number of Products by Stage and Target, 2022

Number of Products by Stage and Mechanism of Action, 2022

Number of Products by Stage and Route of Administration, 2022

Number of Products by Stage and Molecule Type, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by AlphaMab Co Ltd, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by Amarna Therapeutics BV, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by ASC Therapeutics Inc, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by Belief Biomed Inc, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by Biocad, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by Catalyst Biosciences Inc, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by Centessa Pharmaceuticals Plc, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by Chameleon Biosciences Inc, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by Chengdu Rongsheng Pharmaceutical Co Ltd, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by Chia Tai Tianqing Pharmaceutical Group Co Ltd, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by CSL Ltd, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by Daiichi Sankyo Co Ltd, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by Expression Therapeutics Inc, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by Freeline Therapeutics Holdings Plc, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by GC Pharma, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by GeneLeap Biotech, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by GeneVentiv Therapeutics Inc, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by Intellia Therapeutics Inc, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by LFB SA, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by Logicbio Therapeutics Inc, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by Novo Nordisk AS, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by OPKO Health Inc, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by Pfizer Inc, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by RegenxBio Inc, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by Sanofi, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by Sigilon Therapeutics Inc, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by SK Plasma Co Ltd, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by Staidson BioPharma Inc, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by ToolGen Inc, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by UBI Pharma Inc, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by UniQure NV, 2022

Hemophilia B (Factor IX Deficiency) – Pipeline by Zhengzhou Gensciences Inc, 2022

Hemophilia B (Factor IX Deficiency) – Dormant Projects, 2022

Hemophilia B (Factor IX Deficiency) – Dormant Projects, 2022 (Contd..1)

Hemophilia B (Factor IX Deficiency) – Discontinued Products, 2022

Figures

List of Figures

Number of Products under Development for Hemophilia B (Factor IX Deficiency), 2022

Number of Products under Development by Companies, 2022

Number of Products under Development by Universities/Institutes, 2022

Number of Products by Targets, 2022

Number of Products by Stage and Targets, 2022

Number of Products by Mechanism of Actions, 2022

Number of Products by Stage and Mechanism of Actions, 2022

Number of Products by Routes of Administration, 2022

Number of Products by Stage and Routes of Administration, 2022

Number of Products by Molecule Types, 2022

Number of Products by Stage and Molecule Types, 2022

Frequently asked questions

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