Approval of Kalydeco Brings New Hope for CF Patients with G551D Mutation

Pages: 5 Published: February 01, 2012 Report Code: GDHC0055VPT

The viewpoint is an essential source of information and analysis on the KALYDECO (ivacaftor, VX-770) for the treatment of Cystic Fibrosis (CF) patients with G551D mutation. The viewpoint provides insights on the product clinical information and how it will bring new hopes for the CF patients.

Scope

The viewpoint provides impact analysis of approval of Kalydeco in Cystic Fibrosis Patients with G551D mutation. Its scope includes:

Epidemiology

Survival

Current Therapy Options

Unmet Need

Kalydeco – First Disease-Modifying CF Therapy

Clinical Trial Details 3

Cystic Fibrosis Therapeutic Market

Cystic Fibrosis Therapeutic Market – Drivers and Barriers

Reasons to Buy

Inputs on the current treatment options available and the clinical study of the drug. Business strategies development by understanding the current trends and future tends that will driving the global CF therapeutics market. Organize your sales and marketing efforts by identifying the market categories and segments that present maximum opportunities for consolidations, investments and strategic partnerships. How this breakthrough treatment for CF patients with G551D mutation brings new hope.

Table of Contents

1 Table of Contents

1.1 List of Figures

2 Summary

3 Approval of Kalydeco Brings New Hope for CF Patients with G551D Mutation

3.1 Cystic Fibrosis Overview

3.1.1 Disease Overview

3.1.2 Epidemiology

3.1.3 Survival

3.1.4 Current Therapy Options

3.1.5 Unmet Need

3.1.6 Kalydeco – First Disease-Modifying CF Therapy

3.1.7 Clinical Trial Details

3.1.8 Cystic Fibrosis Therapeutic Market

3.1.9 Cystic Fibrosis Therapeutic Market – Drivers and Barriers

4 Appendix

4.1 Methodology

4.1.1 Coverage

4.1.2 Secondary Research

4.1.3 Primary Research

4.1.4 Expert Panel Validation

4.2 Contact Us

4.3 Disclaimer

List of Tables

N/A

List of Figures

Figure 1: CFTR Channel Mutation and Regulation of the Chloride Channel

$500

Can be used by individual purchaser only

$1,500

Can be shared globally by unlimited users within the purchasing corporation e.g. all employees of a single company

Get in touch to find out about our multi-purchase discounts

reportstore@globaldata.com
Tel +44 (0) 20 7947 2960

Every customer’s requirement is unique. We understand that and can customize the report basis your exact research requirements pertaining to market insights, innovation insights, strategy and planning, and competitive intelligence. You can also avail the option of purchasing stand-alone sections of the report or request for a country specific report.

Still undecided about purchasing this report?

Testimonial

“The GlobalData platform is our go-to tool for intelligence services. GlobalData provides an easy way to access comprehensive intelligence data around multiple sectors, which essentially makes it a one-for-all intelligence platform, for tendering and approaching customers.

GlobalData is very customer orientated, with a high degree of personalised services, which benefits everyday use. The highly detailed project intelligence and forecast reports can be utilised across multiple departments and workflow scopes, from operational to strategic level, and often support strategic decisions. GlobalData Analytics and visualisation solutions has contributed positively when preparing management presentations and strategic papers.”

Business Intelligence & Marketing Manager, SAL Heavy Lift

“COVID-19 has caused significant interference to our business and the COVID-19 intelligence from GlobalData has helped us reach better decisions around strategy. These two highlights have helped enormously to understand the projections into the future concerning our business units, we also utilise the project database to source new projects for Liebherr-Werk to use as an additional source to pitch for new business.”

Market Analyst & Management, Liebherr-Werk

Your daily news has saved me a lot of time and keeps me up-to-date with what is happening in the market, I like that you almost always have a link to the source origin. We also use your market data in our Strategic Business Process to support our business decisions. By having everything in one place on the Intelligence Center it has saved me a lot of time versus looking on different sources, the alert function also helps with this.

Head of Key Accounts, Saab AB

Having used several other market research companies, I find that GlobalData manages to provide that ‘difficult-to-get’ market data that others can’t, as well as very diverse and complete consumer surveys.

Marketing Intelligence Manager, Portugal Foods