Approval of Kalydeco Brings New Hope for CF Patients with G551D Mutation

Pages: 5 Published: February 01, 2012 Report Code: GDHC0055VPT

The viewpoint is an essential source of information and analysis on the KALYDECO (ivacaftor, VX-770) for the treatment of Cystic Fibrosis (CF) patients with G551D mutation. The viewpoint provides insights on the product clinical information and how it will bring new hopes for the CF patients.


The viewpoint provides impact analysis of approval of Kalydeco in Cystic Fibrosis Patients with G551D mutation. Its scope includes:



Current Therapy Options

Unmet Need

Kalydeco – First Disease-Modifying CF Therapy

Clinical Trial Details 3

Cystic Fibrosis Therapeutic Market

Cystic Fibrosis Therapeutic Market – Drivers and Barriers

Reasons to Buy

Inputs on the current treatment options available and the clinical study of the drug. Business strategies development by understanding the current trends and future tends that will driving the global CF therapeutics market. Organize your sales and marketing efforts by identifying the market categories and segments that present maximum opportunities for consolidations, investments and strategic partnerships. How this breakthrough treatment for CF patients with G551D mutation brings new hope.

Table of Contents

1 Table of Contents

1.1 List of Figures

2 Summary

3 Approval of Kalydeco Brings New Hope for CF Patients with G551D Mutation

3.1 Cystic Fibrosis Overview

3.1.1 Disease Overview

3.1.2 Epidemiology

3.1.3 Survival

3.1.4 Current Therapy Options

3.1.5 Unmet Need

3.1.6 Kalydeco – First Disease-Modifying CF Therapy

3.1.7 Clinical Trial Details

3.1.8 Cystic Fibrosis Therapeutic Market

3.1.9 Cystic Fibrosis Therapeutic Market – Drivers and Barriers

4 Appendix

4.1 Methodology

4.1.1 Coverage

4.1.2 Secondary Research

4.1.3 Primary Research

4.1.4 Expert Panel Validation

4.2 Contact Us

4.3 Disclaimer

List of Tables


List of Figures

Figure 1: CFTR Channel Mutation and Regulation of the Chloride Channel


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