Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) – Drugs In Development, 2024

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Adrenoleukodystrophy is a disorder that occurs most often in males. It mainly affects the nervous system and the adrenal glands, which are small glands located on top of each kidney. Abetalipoproteinemia is also a kind of adrenoleukodystrophy (adrenomyeloneuropathy/Schilder-Addison complex). Bassen-Kornzweig syndrome is a rare disease passed down through families in which a person is unable to fully absorb dietary fats through the intestines. The disease is caused by a defect in the gene that tells the body to create lipoproteins. Symptoms include curvature of the spine, muscle weakness, and decrease of vision over time. Treatment involves large doses of vitamin supplements containing fat-soluble vitamins.

The Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) drugs in development market research report provide comprehensive information on the therapeutics under development for Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA), and molecule type. The report also covers the descriptive pharmacological action and product description of the therapeutics, and the latest news and press releases. Additionally, the report provides an overview of key players involved in therapeutic development for Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) and features dormant and discontinued products.

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* Certain sections in the report may be removed or altered based on the availability and relevance of data.

Quick View – Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD))
Key Targets
· Thyroid Hormone Receptor Beta; Mitochondrial Pyruvate Carrier; Serine/Threonine Protein Kinase mTOR; Nuclear Factor Erythroid 2 Related Factor 2; Nuclear Factor Kappa B; Peroxisome Proliferator Activated Receptor Gamma; Cholinergic Receptor Nicotinic Subunit; IkappaB Kinase; Acetyl CoA Carboxylase 1; and Acetyl CoA Carboxylase 2
Key Mechanisms of Action
· Thyroid Hormone Receptor Beta Agonist; Mitochondrial Pyruvate Carrier Inhibitor; IkappaB Kinase Inhibitor; Cholinergic Receptor Nicotinic Subunit Antagonist; ATP Binding Cassette Sub Family D Member 1 Activator; Adenosine Monophosphate Activated Protein Kinase Activator; Acetyl CoA Carboxylase 1 Activator; Acetyl CoA Carboxylase 2 Activator; Triggering Receptor Expressed On Myeloid Cells 2 Agonist; and Serine/Threonine Protein Kinase mTOR Inhibitor
Key Routes of Administration
· Oral; Parenteral; Intravenous; Intrathecal; Intracerebral; and Subcutaneous
Key Molecule Types
· Small Molecule; Cell Therapy; Gene Therapy; Monoclonal Antibody; Gene-Modified Cell Therapy; and Synthetic Peptide
Major Companies
· Poxel SA; Orpheris Inc; Shenzhen Geno-Immune Medical Institute; Scenic Biotech BV; ReceptoPharm Inc; Vigil Neuroscience Inc; Viking Therapeutics Inc; SwanBio Therapeutics Inc; Shenzhen Second People's Hospital; and MedDay SA

Scope

  • Therapeutics in Development: Covering 20 molecules, with 15 developed by companies and the rest by universities/institutes.
  • Analysis Parameters: Offering insights by stage of development, drug target, MoA, RoA, and molecule type for a comprehensive overview.
  • Pharmacological Insights: Understand the descriptive pharmacological action of therapeutics.
  • Development History: Access the complete research and development history.
  • Latest News and Press Releases: Stay updated with the latest developments through comprehensive news coverage.

Reasons to Buy

  • Holistic insights: Understand the broad spectrum of Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) therapeutics, aiding strategic decision-making with insights into stages, targets, MoA, RoA and molecule types.
  • Pipeline Exploration: Explore the detailed Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) pipeline, offering nuanced analysis of drug targets, mechanisms of action and routes of administration for varied decision-making.
  • Comprehensive R&D: Access thorough R&D histories, providing a comprehensive understanding of Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) treatments for adaptable decision-making.
  • Save valuable hours: Identify key players steering innovation in therapeutics, enabling strategic partnerships.

Key Players

Apteeus SAS
Autobahn Therapeutics Inc
Celularity Inc
Centers of Biomedical Research Network
Consortium Center for Biomedical Research Network
Duke University
Imstem Biotechnology Inc
MedDay SA
Minoryx Therapeutics sl
Orpheris Inc
Poxel SA
ReceptoPharm Inc
Scenic Biotech BV
Shenzhen Geno-Immune Medical Institute
Shenzhen Second People's Hospital
SwanBio Therapeutics Inc
Vigil Neuroscience Inc
Viking Therapeutics Inc

Table of Contents

Table of Contents

List of Tables

List of Figures

Introduction

Global Markets Direct Report Coverage

Overview

Therapeutics Development

Pipeline Overview

Pipeline by Companies

Pipeline by Universities/Institutes

Drugs Under Development by Companies

Drugs under Development by Universities/Institutes

Therapeutics Assessment

Assessment by Target

Assessment by Mechanism of Action

Assessment by Route of Administration

Assessment by Molecule Type

Companies Involved in Therapeutic Development

Drug Profiles

Dormant Projects

Discontinued Drugs

Product Development Milestones

Appendix

Methodology

Coverage

Secondary Research

Primary Research

Expert Panel Validation

Contact Us

Disclaimer

Table

List of Tables

Number of Drugs under Development, 2024

Number of Drugs under Development by Companies, 2024

Number of Drugs under Development by Universities/Institutes, 2024

Drugs under Development by Companies, 2024

Drugs under Development by Universities/Institutes, 2024

Number of Drugs by Stage and Target, 2024

Number of Drugs by Stage and Mechanism of Action, 2024

Number of Drugs by Stage and Route of Administration, 2024

Number of Drugs by Stage and Molecule Type, 2024

Dormant Projects, 2024

Discontinued Drugs, 2024

Figures

List of Figures

Number of Drugs under Development, 2024

Number of Drugs under Development by Companies, 2024

Number of Drugs under Development by Universities/Institutes, 2024

Number of Drugs by Top 10 Targets, 2024

Number of Drugs by Stage and Top 10 Targets, 2024

Number of Drugs by Top 10 Mechanism of Actions, 2024

Number of Drugs by Stage and Top 10 Mechanism of Actions, 2024

Number of Drugs by Top 10 Routes of Administration, 2024

Number of Drugs by Stage and Top 10 Routes of Administration, 2024

Number of Drugs by Top 10 Molecule Types, 2024

Number of Drugs by Stage and Top 10 Molecule Types, 2024

Frequently asked questions

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