Cystic Fibrosis – Drugs In Development, 2024

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Published: June 05, 2024 Report Code: GDGMDHC23009IDB-L5

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Empower your strategies with our Cystic Fibrosis – Drugs In Development, 2024 report and make more profitable business decisions.

Cystic fibrosis (CF) is an inherited disease that causes mucus to build up and clog some of the body’s organs, particularly the lungs and pancreas. Cystic fibrosis affects the cells that produce mucus, sweat and digestive juices.  Symptoms include wheezing, breathlessness, repeated lung infections, inflamed nasal passages or a stuffy nose, and severe constipation. Risk factors include family history and race (Northern European ancestry). Treatment includes antibiotics, mucus-thinning medications, bronchodilators, and oral pancreatic enzymes.

The Cystic Fibrosis drugs in development market research report provide comprehensive information on the therapeutics under development for Cystic Fibrosis, complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA), and molecule type. The report also covers the descriptive pharmacological action and product description of the therapeutics, and the latest news and press releases. Additionally, the report provides an overview of key players involved in therapeutic development for Cystic Fibrosis and features dormant and discontinued products.

Note:

* This is an “on-demand” report and will be delivered within 2 business days (excluding weekends and holidays) of the purchase.

* Certain sections in the report may be removed or altered based on the availability and relevance of data.

Quick View – Cystic Fibrosis
Key Targets
· Cystic Fibrosis Transmembrane Conductance Regulator; Epithelial Sodium Channel; Anoctamin 1; 30S Ribosomal Subunit (30S RNA); Bacterial Cell Membrane; Advanced Glycosylation End Product Specific Receptor; Bacterial Cell Wall; Mucin 5AC; Mucin 5B; and Mitogen Activated Protein Kinase 14
Key Mechanisms of Action
· Cystic Fibrosis Transmembrane Conductance Regulator Activator; 30S Ribosomal Subunit (30S RNA) Inhibitor; Advanced Glycosylation End Product Specific Receptor Inhibitor; Anoctamin 1 Activator; Bacterial Cell Wall Disruptor; Bacterial Cell Membrane Disruptor; Epithelial Sodium Channel Inhibitor; Mucin 5AC Inhibitor; Mucin 5B Inhibitor; and Mucin Inhibitor
Key Routes of Administration
· Inhalational; Oral; Intravenous; Topical; Subcutaneous; Ophthalmic; Intrapulmonary; Nasal; Intradermal; and Intratracheal
Key Molecule Types
· Small Molecule; Gene Therapy; Biologic; Antisense Oligonucleotide; Recombinant Protein; Synthetic Peptide; Recombinant Enzyme; Peptide; Protein; and Monoclonal Antibody
Major Companies
· Vertex Pharmaceuticals Inc; Sionna Therapeutics Inc; Porosome Therapeutics Inc; Recode Therapeutics Inc; Eloxx Pharmaceuticals Inc; CCM Biosciences Inc; Enterprise Therapeutics Ltd; AbbVie Inc; Biofilm Pharma; and F. Hoffmann-La Roche Ltd

Scope

  • Therapeutics in Development: Covering 128 molecules, with 116 developed by companies and the rest by universities/institutes.

  • Analysis Parameters: Offering insights by stage of development, drug target, MoA, RoA, and molecule type for a comprehensive overview.

  • Pharmacological Insights: Understand the descriptive pharmacological action of therapeutics.

  • Development History: Access the complete research and development history.

  • Latest News and Press Releases: Stay updated with the latest developments through comprehensive news coverage.

Reasons to Buy

  • Holistic insights: Understand the broad spectrum of Cystic Fibrosis therapeutics, aiding strategic decision-making with insights into stages, targets, MoA, RoA and molecule types.

  • Pipeline Exploration: Explore the detailed Cystic Fibrosis pipeline, offering nuanced analysis of drug targets, mechanisms of action and routes of administration for varied decision-making.

  • Comprehensive R&D: Access thorough R&D histories, providing a comprehensive understanding of Cystic Fibrosis treatments for adaptable decision-making.

  • Save valuable hours: Identify key players steering innovation in therapeutics, enabling strategic partnerships.

Key Players

4D Molecular Therapeutics Inc
AbbVie Inc
Aeon Respire Inc
AeroNeph Therapeutics Inc
Airway Therapeutics Inc
Alteron Therapeutics LLC
Anoat Therapeutics
Arcturus Therapeutics Holdings Inc
Aridis Pharmaceuticals Inc
Armata Pharmaceuticals Inc
Arrowhead Pharmaceuticals Inc
Atlantic Healthcare Plc
Avidin Biotechnology Ltd
Biofilm Pharma
BiomX Inc
Boehringer Ingelheim International GmbH
Boston Pharmaceuticals Inc
Branca Bunus Ltd
Carbon Biosciences Inc
Carmine Therapeutics Inc
Chiesi Farmaceutici SpA
ContraFect Corp
CRISPR Therapeutics AG
Cystetic Medicines Inc
Dartmouth College
Destiny Pharma Plc
Eldec Pharmaceuticals Inc
Eloxx Pharmaceuticals Inc
EmphyCorp Inc
Ensysce Biosciences Inc
Enterprise Therapeutics Ltd
Evotec SE
F. Hoffmann-La Roche Ltd
Felix Biotechnology Inc
GeneToBe LLC
Gensaic Inc
George Washington University
Helperby Therapeutics Group Ltd
Hunterian Medicine LLC
ImmunoForge Co Ltd
Insmed Inc
Israel Institute of Technology
Kantify
Kineta Inc
Kither Biotech Srl
Krystal Biotech Inc
Laurent Pharmaceuticals Inc
Loxegen Pty Ltd
MannKind Corp
MD Healthcare Inc
Metagenomi Inc
Microbion Corp
Moderna Inc
Nabriva Therapeutics Plc
NuPeak Therapeutics Inc
Nuravax Inc
Omnispirant Ltd
Oregon State University
OrPro Therapeutics Inc
Peptilogics Inc
Porosome Therapeutics Inc
Prime Medicine Inc
Prolong Pharmaceuticals LLC
PureIMS BV
Pylum Biosciences Inc
RAGE Biotech Pty Ltd
Rare Partners Srl
Recode Therapeutics Inc
Respirion Pharmaceuticals Pty Ltd
RS BioTherapeutics Inc
Saliogen Therapeutics Inc
SciClone Pharmaceuticals Holdings Ltd
Sionna Therapeutics Inc
SOLA Biosciences LLC
Southern Research Institute
Specific Biologics Inc
Spexis AG
Spirovant Sciences Inc
SpliSense Ltd
Synovo GmbH
Tavanta Therapeutics Inc
Telum Therapeutics SL
TGV-Inhalonix Inc
Therapeutic Systems Research Laboratories Inc
Thirty Respiratory Ltd
UAB Minority Health and Health Equity Research Center
University of Barcelona
University of Maryland
University of North Carolina
University of Southampton
University of Wollongong
Vast Therapeutics Inc
Verona Pharma Plc
Vertex Pharmaceuticals Inc
VGSK Technologies Inc
Vironika LLC
Windtree Therapeutics Inc
Xellia Pharmaceuticals ApS
Zambon Co SpA
Zata Pharmaceuticals Inc
Ziphius Vaccines NV

Table of Contents

Table of Contents

List of Tables

List of Figures

Introduction

Global Markets Direct Report Coverage

Overview

Therapeutics Development

Pipeline Overview

Pipeline by Companies

Pipeline by Universities/Institutes

Drugs Under Development by Companies

Drugs under Development by Universities/Institutes

Therapeutics Assessment

Assessment by Target

Assessment by Mechanism of Action

Assessment by Route of Administration

Assessment by Molecule Type

Companies Involved in Therapeutic Development

Drug Profiles

Dormant Projects

Discontinued Drugs

Product Development Milestones

Appendix

Methodology

Coverage

Secondary Research

Primary Research

Expert Panel Validation

Contact Us

Disclaimer

Table

List of Tables

Number of Drugs under Development, 2024

Number of Drugs under Development by Companies, 2024

Number of Drugs under Development by Universities/Institutes, 2024

Drugs under Development by Companies, 2024

Drugs under Development by Universities/Institutes, 2024

Number of Drugs by Stage and Target, 2024

Number of Drugs by Stage and Mechanism of Action, 2024

Number of Drugs by Stage and Route of Administration, 2024

Number of Drugs by Stage and Molecule Type, 2024

Dormant Projects, 2024

Discontinued Drugs, 2024

Figures

List of Figures

Number of Drugs under Development, 2024

Number of Drugs under Development by Companies, 2024

Number of Drugs under Development by Universities/Institutes, 2024

Number of Drugs by Top 10 Targets, 2024

Number of Drugs by Stage and Top 10 Targets, 2024

Number of Drugs by Top 10 Mechanism of Actions, 2024

Number of Drugs by Stage and Top 10 Mechanism of Actions, 2024

Number of Drugs by Top 10 Routes of Administration, 2024

Number of Drugs by Stage and Top 10 Routes of Administration, 2024

Number of Drugs by Top 10 Molecule Types, 2024

Number of Drugs by Stage and Top 10 Molecule Types, 2024

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