Duchenne Muscular Dystrophy – Drugs In Development, 2024

Powered by

Unlock hidden opportunities in the Pharmaceuticals industry

$2000
Buy Report

Published: June 05, 2024 Report Code: GDGMDHC23008IDB-L5

Select Item

Empower your strategies with our Duchenne Muscular Dystrophy – Drugs In Development, 2024 report and make more profitable business decisions.

Duchenne muscular dystrophy (DMD) is a genetic disorder that causes muscles to gradually weaken over time. Signs and symptoms of DMD include fatigue, learning difficulties, intellectual disability, muscle weakness, and progressive difficulty walking. Risk factors include gender and family history. Treatments include steroid medication, respiratory therapy, and surgery.

The Duchenne Muscular Dystrophy drugs in development market research report provide comprehensive information on the therapeutics under development for Duchenne Muscular Dystrophy, complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA), and molecule type. The report also covers the descriptive pharmacological action and product description of the therapeutics, and the latest news and press releases. Additionally, the report provides an overview of key players involved in therapeutic development for Duchenne Muscular Dystrophy and features dormant and discontinued products.

Note:

* This is an “on-demand” report and will be delivered within 2 business days (excluding weekends and holidays) of the purchase.

* Certain sections in the report may be removed or altered based on the availability and relevance of data.

Quick View – Duchenne Muscular Dystrophy
Key Targets
· Dystrophin; Utrophin; Glucocorticoid Receptor; Integrin Alpha 7; Growth/Differentiation Factor 8; Androgen Receptor; Cystic Fibrosis Transmembrane Conductance Regulator; Mas Related G Protein Coupled Receptor MRG; AP2 Associated Protein Kinase 1; and Adenosine Monophosphate Activated Protein Kinase
Key Mechanisms of Action
· Dystrophin Activator; Utrophin Activator; Dystrophin Replacement; Glucocorticoid Receptor Agonist; Growth/Differentiation Factor 8 Inhibitor; Integrin Alpha 7 Agonist; Integrin Beta 1 Agonist; Hematopoietic Prostaglandin D Synthase Inhibitor; Androgen Receptor Agonist; and AP2 Associated Protein Kinase 1 Inhibitor
Key Routes of Administration
· Intravenous; Oral; Subcutaneous; Parenteral; Intramuscular; Inhalational; Intrathecal; Ophthalmic; Intraarticular; and Intracoronary
Key Molecule Types
· Small Molecule; Antisense Oligonucleotide; Gene Therapy; Cell Therapy; Oligonucleotide; Gene-Modified Cell Therapy; Fusion Protein; Synthetic Peptide; Recombinant Protein; and Biologic
Major Companies
· Sarepta Therapeutics Inc; Dyne Therapeutics Inc; Entrada Therapeutics Inc; Daiichi Sankyo Co Ltd; Avidity Biosciences Inc; NS Pharma Inc; Sarcomed AB; Pepgen Inc; Suzhou GenAssist Therapeutics Co Ltd; and University of California Los Angeles

Scope

  • Therapeutics in Development: Covering 198 molecules, with 175 developed by companies and the rest by universities/institutes.

  • Analysis Parameters: Offering insights by stage of development, drug target, MoA, RoA, and molecule type for a comprehensive overview.

  • Pharmacological Insights: Understand the descriptive pharmacological action of therapeutics.

  • Development History: Access the complete research and development history.

  • Latest News and Press Releases: Stay updated with the latest developments through comprehensive news coverage.

Reasons to Buy

  • Holistic insights: Understand the broad spectrum of Duchenne Muscular Dystrophy therapeutics, aiding strategic decision-making with insights into stages, targets, MoA, RoA and molecule types.

  • Pipeline Exploration: Explore the detailed Duchenne Muscular Dystrophy pipeline, offering nuanced analysis of drug targets, mechanisms of action and routes of administration for varied decision-making.

  • Comprehensive R&D: Access thorough R&D histories, providing a comprehensive understanding of Duchenne Muscular Dystrophy treatments for adaptable decision-making.

  • Save valuable hours: Identify key players steering innovation in therapeutics, enabling strategic partnerships.

Key Players

AAVogen Inc
ADEL Inc
Allagium therapeutics Inc
Alpha Anomeric
American CryoStem Corp
AMO Pharma Ltd
Anagenesis Biotechnologies SAS
Antisense Therapeutics Ltd
ARMGO Pharma Inc
ART BioScience
Astria Therapeutics Inc
AUM LifeTech Inc
Autotac Bio Inc
Avidity Biosciences Inc
Axolo Pharma Inc
BioIncept LLC
Bioleaders Corp
BioMarin Pharmaceutical Inc
Biophytis SA
CANbridge Life Sciences Ltd
Capricor Therapeutics Inc
ChemIcare Srl
Chengdu Fanxi Biopharma Co Ltd
Chengdu Genevector Biotechnology Co Ltd
Code Biotherapeutics Inc
Consortium.AI
Constant Therapeutics LLC
Cumberland Pharmaceuticals Inc
Curamys Co Ltd
Cure Rare Disease
Daiichi Sankyo Co Ltd
DR.Noah Biotech Inc
Dyne Therapeutics Inc
Dystrogen Therapeutics SA
ECM Therapeutics Inc
Edgewise Therapeutics Inc
Editas Medicine Inc
Eli Lilly and Co
Eloxx Pharmaceuticals Inc
Encell Co Ltd
Entrada Therapeutics Inc
Epirium Bio Inc
EspeRare Foundation
FibroGenesis LLC
Fulcrum Therapeutics Inc
Genethon SA
Harvard University
hC Bioscience Inc
HuidaGene Therapeutics Co Ltd
ImmunoForge Co Ltd
Imstem Biotechnology Inc
Inmune Bio Inc
InnoBioscience LLC
Insmed Inc
Intas Pharmaceuticals Ltd
IPS Heart Inc
Italfarmaco SpA
Ixchel Pharma LLC
J2H Biotech
JAR of Hope
Juvena Therapeutics Inc
Kaneka Corp
Keros Therapeutics Inc
Korea Pharma Co Ltd
Korea University
KSbitugen Co Ltd
LambdaGen Therapeutics
Les Laboratoires Servier SAS
Locanabio Inc
Ludi Therapeutics
MetrioPharm AG
Mitobridge Inc
Mitochon Pharmaceuticals Inc
MitoRx Therapeutics Ltd
MyoGene Bio LLC
Myogenica Inc
Myos Inc
Myosana Therapeutics Inc
Nippon Shinyaku Co Ltd
Northwestern University
Novo Biosciences Inc
NS Pharma Inc
NTrans Technologies BV
OliPass Corporation
OMEICOS Therapeutics GmbH
Oncotelic Therapeutics Inc
Orna Therapeutics Inc
Pepgen Inc
PeptiDream Inc
Perelman School of Medicine at the University of Pennsylvania
Pfizer Inc
Pliant Therapeutics Inc
Prime Medicine Inc
Progenitor Therapeutics Ltd
Prothelia Inc
PTC Therapeutics Inc
PYC Therapeutics Ltd
Quince Therapeutics Inc
Ractigen Therapeutics Inc
RASRx LLC
RegenxBio Inc
ReoStem LLC
Ridgeline Therapeutics LLC
Royal Holloway University of London
Santhera Pharmaceuticals Holding AG
Sarcomed AB
Sarepta Therapeutics Inc
Satellos Bioscience Inc
SiVEC Biotechnologies LLC
Solid Biosciences Inc
SOM Biotech SL
Sqy Therapeutics SA
Stanford University
Stealth BioTherapeutics Inc.
Stem Cells of Arabia
SteroTherapeutics LLC
Strykagen Corp
Sutura Therapeutics Ltd
Suzhou GenAssist Therapeutics Co Ltd
Taiho Pharmaceutical Co Ltd
Technical University of Munich
Tevard Biosciences LLC
The Hospital for Sick Children
Tivorsan Pharmaceuticals Inc
Tolerion Inc
Triplex Therapeutics Inc
UGISense AG
Ultragenyx Pharmaceutical Inc
University Children's Hospital Basel
University of Alberta
University of California Los Angeles
University of Exeter
University of Pennsylvania
University of Queensland
University of Wisconsin Madison
Vertex Pharmaceuticals Inc
Vita Therapeutics Inc
Vitti Labs LLC
Wave Life Sciences Ltd
Zata Pharmaceuticals Inc

Table of Contents

Table of Contents

List of Tables

List of Figures

Introduction

Global Markets Direct Report Coverage

Overview

Therapeutics Development

Pipeline Overview

Pipeline by Companies

Pipeline by Universities/Institutes

Drugs Under Development by Companies

Drugs under Development by Universities/Institutes

Therapeutics Assessment

Assessment by Target

Assessment by Mechanism of Action

Assessment by Route of Administration

Assessment by Molecule Type

Companies Involved in Therapeutic Development

Drug Profiles

Dormant Projects

Discontinued Drugs

Product Development Milestones

Appendix

Methodology

Coverage

Secondary Research

Primary Research

Expert Panel Validation

Contact Us

Disclaimer

Table

List of Tables

Number of Drugs under Development, 2024

Number of Drugs under Development by Companies, 2024

Number of Drugs under Development by Universities/Institutes, 2024

Drugs under Development by Companies, 2024

Drugs under Development by Universities/Institutes, 2024

Number of Drugs by Stage and Target, 2024

Number of Drugs by Stage and Mechanism of Action, 2024

Number of Drugs by Stage and Route of Administration, 2024

Number of Drugs by Stage and Molecule Type, 2024

Dormant Projects, 2024

Discontinued Drugs, 2024

Figures

List of Figures

Number of Drugs under Development, 2024

Number of Drugs under Development by Companies, 2024

Number of Drugs under Development by Universities/Institutes, 2024

Number of Drugs by Top 10 Targets, 2024

Number of Drugs by Stage and Top 10 Targets, 2024

Number of Drugs by Top 10 Mechanism of Actions, 2024

Number of Drugs by Stage and Top 10 Mechanism of Actions, 2024

Number of Drugs by Top 10 Routes of Administration, 2024

Number of Drugs by Stage and Top 10 Routes of Administration, 2024

Number of Drugs by Top 10 Molecule Types, 2024

Number of Drugs by Stage and Top 10 Molecule Types, 2024

Frequently asked questions

Currency USD
$2,000

Can be used by individual purchaser only

Most Popular
$4,000

Can be shared by unlimited users within one corporate location e.g. a regional office

$6,000

Can be shared globally by unlimited users within the purchasing corporation e.g. all employees of a single company

Add to Basket

Undecided about purchasing this report?

Enquire Before Buying

Get in touch to find out about multi-purchase discounts

reportstore@globaldata.com
Tel +44 20 7947 2745

See what our customers are saying
testimonial-image
testimonial-image
testimonial-image
testimonial-image
testimonial-image
testimonial-image
testimonial-image

“The GlobalData platform is our go-to tool for intelligence services. GlobalData provides an easy way to access comprehensive intelligence data around multiple sectors, which essentially makes it a one-for-all intelligence platform, for tendering and approaching customers.

GlobalData is very customer orientated, with a high degree of personalised services, which benefits everyday use. The highly detailed project intelligence and forecast reports can be utilised across multiple departments and workflow scopes, from operational to strategic level, and often support strategic decisions. GlobalData Analytics and visualisation solutions has contributed positively when preparing management presentations and strategic papers.”

 Business Intelligence & Marketing Manager, SAL Heavy Lift

“COVID-19 has caused significant interference to our business and the COVID-19 intelligence from GlobalData has helped us reach better decisions around strategy. These two highlights have helped enormously to understand the projections into the future concerning our business units, we also utilise the project database to source new projects for Liebherr-Werk to use as an additional source to pitch for new business.”

 Market Analyst & Management, Liebherr-Werk

Your daily news has saved me a lot of time and keeps me up-to-date with what is happening in the market, I like that you almost always have a link to the source origin. We also use your market data in our Strategic Business Process to support our business decisions. By having everything in one place on the Intelligence Center it has saved me a lot of time versus looking on different sources, the alert function also helps with this.

 Head of Key Accounts, Saab AB

Having used several other market research companies, I find that GlobalData manages to provide that ‘difficult-to-get’ market data that others can’t, as well as very diverse and complete consumer surveys.

 Marketing Intelligence Manager, Portugal Foods

Our experience with GlobalData has been very good, from the platform itself to the people. I find that the analysts and the account team have a high level of customer focus and responsiveness and therefore I can always rely on. The platform is more holistic than other providers. It is convenient and almost like a one stop shop. The pricing suite is highly competitive and value for our organisation.

I like reports that inform new segments such as the analysis on generation Z, millennials, the impact of COVID 19 to our banking customers and their new channel habits. Secondly the specialist insight on affluent sector significantly increases our understanding about this group of customers. The combination of those give us depth and breadth of the evolving market.

I’m in the business of answering and helping people make decisions so with the intelligence center I can do that, effectively and efficiently. I can share quickly key insights that answer and satisfy our country stakeholders by giving them many quality studies and primary research about competitive landscape beyond the outlook of our bank. It helps me be seen as an advisory partner and that makes a big difference. A big benefit of our subscription is that no one holds the whole data and because it allows so many people, so many different parts of our organisation have access, it enables all teams to have the same level of knowledge and decision support.

 Head of Customer Insight and Research, Standard Chartered

“I know that I can always rely on Globaldata’s work when I’m searching for the right consumer and market insights. I use Globaldata insights to understand the changing market & consumer landscape and help create better taste & wellbeing solutions for our customers in food, beverage and healthcare industries.

Globaldata has the right data and the reports are of very high quality compared to your competitors. Globaldata not only has overall market sizes & consumer insights on food & beverages but also provides insights at the ingredient & flavour level. That is key for B2B companies like Givaudan. This way we understand our customers’ business and also gain insight to our unique industry”

 Head of Consumer Sensory Insights, Givaudan

GlobalData provides a great range of information and reports on various sectors that is highly relevant, timely, easy to access and utilise.  The reports and data dashboards help engagement with clients; they provide valuable industry and market insights that can enrich client conversations and can help in the shaping of value propositions. Moreover, using GlobalData products has helped increase my knowledge of the finance sector, the players within it, and the general threats and opportunities.

I find the consumer surveys that are carried out to be extremely beneficial and not something I have seen anywhere else. They provided an insightful view of why and which consumers take (or don’t) particular financial products. This can help shape conversations with clients to ensure they make the right strategic decisions for their business.

One of the challenges I have found is that data in the payments space is often piecemeal. With GD all of the data I need is in one place, but it also comes with additional market reports that provide useful extra context and information. Having the ability to set-up alerts on relevant movements in the industry, be it competitors or customers, and have them emailed directly to me, ensures I get early sight of industry activity and don’t have to search for news.

 Senior Account Manager, TSYS

Related reports

View more Duchenne Muscular Dystrophy reports
Pharmaceuticals
New
Reflux Esophagitis (Gastroesophageal Reflux Disease): Market View, Current and Future…
$3,495 | June 2026
Pharmaceuticals
New
IgA Nephropathy (Berger’s Disease): Market View, Current and Future Competitive…
$3,495 | June 2026
Pharmaceuticals
New
Hepatocellular Carcinoma (HCC): Epidemiology Report and Forecast to 2035
$9,995 | June 2026
Go even deeper with GlobalData Intelligence Center

Every Company Report we produce is powered by the GlobalData Intelligence Center.

Subscribing to our intelligence platform means you can monitor developments at Duchenne Muscular Dystrophy – Drugs In Development, 2024 in real time.

  • Access a live Duchenne Muscular Dystrophy – Drugs In Development, 2024 dashboard for 12 months, with up-to-the-minute insights.
  • Fuel your decision making with real-time deal coverage and media activity.
  • Turn insights on financials, deals, products and pipelines into powerful agents of commercial advantage.
Tell me more