Hemophilia A (Factor VIII Deficiency) – Drugs In Development, 2024

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Published: June 05, 2024 Report Code: GDGMDHC23076IDB-L5

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Hemophilia A is an X-linked recessive disorder caused by deficiency of functional plasma clotting factor VIII (FVIII), which may be inherited or arise from spontaneous mutation. Depending on the level of FVIII activity, patients with hemophilia may present with easy bruising, inadequate clotting of traumatic injury, or in the case of severe hemophilia, spontaneous hemorrhage. Symptoms may include bleeding into joints, with associated pain and swelling, blood in the urine or stool, bruising, gastrointestinal tract and urinary tract hemorrhage, nosebleeds, spontaneous bleeding, and prolonged bleeding from cuts, tooth extraction, and surgery.

The Hemophilia A (Factor VIII Deficiency) drugs in development market research report provide comprehensive information on the therapeutics under development for Hemophilia A (Factor VIII Deficiency), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA), and molecule type. The report also covers the descriptive pharmacological action and product description of the therapeutics, and the latest news and press releases. Additionally, the report provides an overview of key players involved in therapeutic development for Hemophilia A (Factor VIII Deficiency) and features dormant and discontinued products.

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* This is an “on-demand” report and will be delivered within 2 business days (excluding weekends and holidays) of the purchase.

* Certain sections in the report may be removed or altered based on the availability and relevance of data.

Quick View – Hemophilia A (Factor VIII Deficiency)
Key Targets
· Coagulation Factor VIII; Coagulation Factor IX; Coagulation Factor X; Coagulation Factor VII; Tissue Factor Pathway Inhibitor; Von Willebrand Factor; Vitamin K Dependent Protein C; and Antithrombin III
Key Mechanisms of Action
· Coagulation Factor VIII Activator; Coagulation Factor VIII Replacement; Coagulation Factor IX Activator; Coagulation Factor X Activator; Coagulation Factor VII Replacement; Tissue Factor Pathway Inhibitor Inhibitor; Von Willebrand Factor Inhibitor; Von Willebrand Factor Replacement; Vitamin K Dependent Protein C Inhibitor; and Coagulation Factor IX Inhibitor
Key Routes of Administration
· Intravenous; Subcutaneous; Parenteral; Intravenous Bolus; Oral; Intravenous Drip; and Intramuscular
Key Molecule Types
· Gene Therapy; Recombinant Protein; Gene-Modified Cell Therapy; Monoclonal Antibody; Fusion Protein; Aptamer; Antibody; Blood Derivative; Biologic; and Antisense RNAi Oligonucleotide
Major Companies
· Novo Nordisk AS; Beijing Neoletix Biological Technology Co Ltd; Takeda Pharmaceutical Co Ltd; Zhengzhou Gensciences Inc; Ascension Healthcare Plc; ASC Therapeutics Inc; Chia Tai Tianqing Pharmaceutical Group Co Ltd; Expression Therapeutics Inc; G&P Bioscience Co Ltd; and Pfizer Inc

Scope

  • Therapeutics in Development: Covering 102 molecules, with 95 developed by companies and the rest by universities/institutes.

  • Analysis Parameters: Offering insights by stage of development, drug target, MoA, RoA, and molecule type for a comprehensive overview.

  • Pharmacological Insights: Understand the descriptive pharmacological action of therapeutics.

  • Development History: Access the complete research and development history.

  • Latest News and Press Releases: Stay updated with the latest developments through comprehensive news coverage.

Reasons to Buy

  • Holistic insights: Understand the broad spectrum of Hemophilia A (Factor VIII Deficiency) therapeutics, aiding strategic decision-making with insights into stages, targets, MoA, RoA and molecule types.

  • Pipeline Exploration: Explore the detailed Hemophilia A (Factor VIII Deficiency) pipeline, offering nuanced analysis of drug targets, mechanisms of action and routes of administration for varied decision-making.

  • Comprehensive R&D: Access thorough R&D histories, providing a comprehensive understanding of Hemophilia A (Factor VIII Deficiency) treatments for adaptable decision-making.

  • Save valuable hours: Identify key players steering innovation in therapeutics, enabling strategic partnerships.

Key Players

AlphaMab Co Ltd
Alveron Pharma
Amarna Therapeutics BV
Anyuan Pharmaceutical Technology (Shanghai) Co Ltd
ASC Therapeutics Inc
Ascension Healthcare Plc
Atomwise Inc
Band Therapeutics LLC
Baudax Bio Inc
Baylor College of Medicine
Beijing Neoletix Biological Technology Co Ltd
Beijing Northland Biotech Co Ltd
Beijing Tiantan Biological Products Co Ltd
Belief Biomed Inc
Biocad
BioMarin Pharmaceutical Inc
Biotest AG
BloodCenter of Wisconsin
CANbridge Life Sciences Ltd
Casebia Therapeutics LLP
CellGenTech Inc
Centessa Pharmaceuticals Plc
Centre for Stem Cell Research
Chameleon Biosciences Inc
Chia Tai Tianqing Pharmaceutical Group Co Ltd
Chugai Pharmaceutical Co Ltd
Daiichi Sankyo Co Ltd
Dnarx LLC
EpiVax Inc
Equilibra Bioscience LLC
Exegenesis Bio Inc
Expression Therapeutics Inc
G&P Bioscience Co Ltd
GC Biopharma Corp
GeneOne Life Science Inc
Generation Bio Co
GeneVentiv Therapeutics Inc
Hebei Da'an Pharmaceutical Co Ltd
ID Pharma Co Ltd
Idogen AB
Innovare R & D SA De CV
Intas Pharmaceuticals Ltd
Intellia Therapeutics Inc
Kaifeng Pharmaceutical (Group) Co Ltd
Kymab Ltd
LambdaGen Therapeutics
LFB SA
MediciNova Inc
Metagenomi Inc
NovalGen Ltd
Novo Nordisk AS
Octapharma AG
OPKO Health Inc
Pangen Biotech Inc
Pfizer Inc
Pharming Group NV
Poseida Therapeutics Inc
ProFactor Pharma Ltd
Rani Therapeutics LLC
Sanofi
Seattle Children’s Research Institute
Shandong Taibang Biological Products Co Ltd
Shanghai BDgene Therapeutics Co Ltd
Shenzhen Geno-Immune Medical Institute
Sichuan Yuanda Shuyang Pharmaceutical Co Ltd
Sichuan Zhishan Weixin Biotechnology Co Ltd
Sigilon Therapeutics Inc
Sino Biopharmaceutical Ltd
SinoCelltech Group Ltd
SK Plasma Co Ltd
Spark Therapeutics Inc
Staidson BioPharma Inc
State University of New York at Buffalo
Suzhou Huayi Liangjian Biotechnology Co Ltd
Suzhou Ribo Life Sciences Co Ltd
Symvivo Inc
Takeda Pharmaceutical Co Ltd
TiumBio Co Ltd
Ultragenyx Pharmaceutical Inc
University of Florida
Worg Pharmaceuticals Hangzhou Co Ltd
Zhengzhou Gensciences Inc

Table of Contents

Table of Contents

List of Tables

List of Figures

Introduction

Global Markets Direct Report Coverage

Overview

Therapeutics Development

Pipeline Overview

Pipeline by Companies

Pipeline by Universities/Institutes

Drugs Under Development by Companies

Drugs under Development by Universities/Institutes

Therapeutics Assessment

Assessment by Target

Assessment by Mechanism of Action

Assessment by Route of Administration

Assessment by Molecule Type

Companies Involved in Therapeutic Development

Drug Profiles

Dormant Projects

Discontinued Drugs

Product Development Milestones

Appendix

Methodology

Coverage

Secondary Research

Primary Research

Expert Panel Validation

Contact Us

Disclaimer

Table

List of Tables

Number of Drugs under Development, 2024

Number of Drugs under Development by Companies, 2024

Number of Drugs under Development by Universities/Institutes, 2024

Drugs under Development by Companies, 2024

Drugs under Development by Universities/Institutes, 2024

Number of Drugs by Stage and Target, 2024

Number of Drugs by Stage and Mechanism of Action, 2024

Number of Drugs by Stage and Route of Administration, 2024

Number of Drugs by Stage and Molecule Type, 2024

Dormant Projects, 2024

Discontinued Drugs, 2024

Figures

List of Figures

Number of Drugs under Development, 2024

Number of Drugs under Development by Companies, 2024

Number of Drugs under Development by Universities/Institutes, 2024

Number of Drugs by Top 10 Targets, 2024

Number of Drugs by Stage and Top 10 Targets, 2024

Number of Drugs by Top 10 Mechanism of Actions, 2024

Number of Drugs by Stage and Top 10 Mechanism of Actions, 2024

Number of Drugs by Top 10 Routes of Administration, 2024

Number of Drugs by Stage and Top 10 Routes of Administration, 2024

Number of Drugs by Top 10 Molecule Types, 2024

Number of Drugs by Stage and Top 10 Molecule Types, 2024

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