Muscular Dystrophy – Drugs In Development, 2024

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Published: June 05, 2024 Report Code: GDGMDHC23059IDB-L5

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Empower your strategies with our Muscular Dystrophy – Drugs In Development, 2024 report and make more profitable business decisions.

Muscular dystrophy is a group of diseases in which muscle fibers are unusually susceptible to damage. These damaged muscles become progressively weaker. Symptoms usually appear before age 6 and may appear as early as infancy. They may include fatigue, learning difficulties, intellectual disability, muscle weakness, and progressive difficulty walking.

The Muscular Dystrophy drugs in development market research report provide comprehensive information on the therapeutics under development for Muscular Dystrophy, complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA), and molecule type. The report also covers the descriptive pharmacological action and product description of the therapeutics, and the latest news and press releases. Additionally, the report provides an overview of key players involved in therapeutic development for Muscular Dystrophy and features dormant and discontinued products.

Note:

* This is an “on-demand” report and will be delivered within 2 business days (excluding weekends and holidays) of the purchase.

* Certain sections in the report may be removed or altered based on the availability and relevance of data.

Quick View – Muscular Dystrophy
Key Targets
· Double Homeobox Protein 4; Myotonin Protein Kinase; Dysferlin; AP2 Associated Protein Kinase 1; Calpain 3; Integrin Alpha 7; Laminin Subunit Alpha 2; Gamma Sarcoglycan ; Integrin Beta 1; and RNA
Key Mechanisms of Action
· Double Homeobox Protein 4 Inhibitor; Myotonin Protein Kinase Inhibitor; Dysferlin Activator; Calpain 3 Activator; AP2 Associated Protein Kinase 1 Inhibitor; Gamma Sarcoglycan Activator; Integrin Beta 1 Agonist; Integrin Alpha 7 Agonist; Laminin Subunit Alpha 2 Activator; and Polyadenylate Binding Protein 2 Inhibitor
Key Routes of Administration
· Oral; Intravenous; Parenteral; Intramuscular; Subcutaneous; Inhalational; Sublingual; and Topical
Key Molecule Types
· Small Molecule; Gene Therapy; Antisense Oligonucleotide; Antisense RNAi Oligonucleotide; Cell Therapy; Monoclonal Antibody; Gene-Modified Cell Therapy; RNAi Gene Therapy; Synthetic Peptide; and Monoclonal Antibody Conjugated
Major Companies
· Sarepta Therapeutics Inc; Kate Therapeutics Inc; Modalis Therapeutics Corp; Atamyo Therapeutics SAS; Vertex Pharmaceuticals Inc; Vita Therapeutics Inc; University of Florida; University of Montpellier; Satellos Bioscience Inc; and Recursion Pharmaceuticals Inc

Scope

  • Therapeutics in Development: Covering 130 molecules, with 114 developed by companies and the rest by universities/institutes.

  • Analysis Parameters: Offering insights by stage of development, drug target, MoA, RoA, and molecule type for a comprehensive overview.

  • Pharmacological Insights: Understand the descriptive pharmacological action of therapeutics.

  • Development History: Access the complete research and development history.

  • Latest News and Press Releases: Stay updated with the latest developments through comprehensive news coverage.

Reasons to Buy

  • Holistic insights: Understand the broad spectrum of Muscular Dystrophy therapeutics, aiding strategic decision-making with insights into stages, targets, MoA, RoA and molecule types.

  • Pipeline Exploration: Explore the detailed Muscular Dystrophy pipeline, offering nuanced analysis of drug targets, mechanisms of action and routes of administration for varied decision-making.

  • Comprehensive R&D: Access thorough R&D histories, providing a comprehensive understanding of Muscular Dystrophy treatments for adaptable decision-making.

  • Save valuable hours: Identify key players steering innovation in therapeutics, enabling strategic partnerships.

Key Players

Achelios Therapeutics Inc
Altay Therapeutics Inc
Amicus Therapeutics Inc
AMO Pharma Ltd
Anima Biotech Inc
Antisense Therapeutics Ltd
Armatus Bio LLC
Arrowhead Pharmaceuticals Inc
ARTHEx Biotech SL
Asklepios BioPharmaceutical Inc
Astellas Gene Therapies
Atamyo Therapeutics SAS
Avidity Biosciences Inc
Base4 Biotechnology Inc
Beech Tree Labs Inc
Benitec Biopharma Inc
Biophytis SA
CalyGene Biotechnology Inc
CANbridge Life Sciences Ltd
Casma Therapeutics Inc
Celularity Inc
Children's National Hospital
Constant Therapeutics LLC
CRISPR Therapeutics AG
Debiopharm International SA
Denali Therapeutics Inc
Design Therapeutics Inc
DR.Noah Biotech Inc
Dyne Therapeutics Inc
ECM Therapeutics Inc
Edgewise Therapeutics Inc
EditForce Inc
Elixirgen Therapeutics Inc
Entrada Therapeutics Inc
Enzerna Biosciences LLC
Epicrispr Biotechnologies Inc
Exodos Life Sciences Limited Partnership
Expansion Therapeutics Inc
F. Hoffmann-La Roche Ltd
Facio Therapies BV
Faze medicines
Fred Hutchinson Cancer Research Center
Fulcrum Therapeutics Inc
Generian Pharmaceuticals Inc
Harmony Biosciences Holdings Inc
Healx Ltd
Hope Biosciences LLC
Juvena Therapeutics Inc
Kantify
Kate Therapeutics Inc
LinkedUp Bioscience Inc
Locanabio Inc
Loqus23 Therapeutics Ltd
Lupin Ltd
Mission Therapeutics Ltd
ML Bio Solutions Inc
Modalis Therapeutics Corp
Myocea Inc
Myogem Health Company SL
MyoPax GmbH
Myos Inc
Nationwide Children's Hospital
Neuvivo Inc
Nexien Biopharma Inc
Nippon Shinyaku Co Ltd
Osaka University
Osaka University Hospital
Pasithea Therapeutics Corp
Pepgen Inc
Pfizer Inc
Prime Medicine Inc
Prothelia Inc
QiXia Decode Therapeutics
Recursion Pharmaceuticals Inc
Renogenyx Inc
SanBio Co Ltd
Sanofi
Santhera Pharmaceuticals Holding AG
Sarcomed AB
Sarepta Therapeutics Inc
Satellos Bioscience Inc
Scriptr Global Inc
SEAL Therapeutics AG
Seelos Therapeutics
Inc.
Siwa Therapeutics Inc
Syros Pharmaceuticals Inc
The Scripps Research Institute
The University of Nottingham
Triplet Therapeutics Inc
University of Florida
University of Illinois
University of Michigan
University of Minnesota
University of Montpellier
University of Rochester Medical Center
Vertex Pharmaceuticals Inc
Vita Therapeutics Inc

Table of Contents

Table of Contents

List of Tables

List of Figures

Introduction

Global Markets Direct Report Coverage

Overview

Therapeutics Development

Pipeline Overview

Pipeline by Companies

Pipeline by Universities/Institutes

Drugs Under Development by Companies

Drugs under Development by Universities/Institutes

Therapeutics Assessment

Assessment by Target

Assessment by Mechanism of Action

Assessment by Route of Administration

Assessment by Molecule Type

Companies Involved in Therapeutic Development

Drug Profiles

Dormant Projects

Discontinued Drugs

Product Development Milestones

Appendix

Methodology

Coverage

Secondary Research

Primary Research

Expert Panel Validation

Contact Us

Disclaimer

Table

List of Tables

Number of Drugs under Development, 2024

Number of Drugs under Development by Companies, 2024

Number of Drugs under Development by Universities/Institutes, 2024

Drugs under Development by Companies, 2024

Drugs under Development by Universities/Institutes, 2024

Number of Drugs by Stage and Target, 2024

Number of Drugs by Stage and Mechanism of Action, 2024

Number of Drugs by Stage and Route of Administration, 2024

Number of Drugs by Stage and Molecule Type, 2024

Dormant Projects, 2024

Discontinued Drugs, 2024

Figures

List of Figures

Number of Drugs under Development, 2024

Number of Drugs under Development by Companies, 2024

Number of Drugs under Development by Universities/Institutes, 2024

Number of Drugs by Top 10 Targets, 2024

Number of Drugs by Stage and Top 10 Targets, 2024

Number of Drugs by Top 10 Mechanism of Actions, 2024

Number of Drugs by Stage and Top 10 Mechanism of Actions, 2024

Number of Drugs by Top 10 Routes of Administration, 2024

Number of Drugs by Stage and Top 10 Routes of Administration, 2024

Number of Drugs by Top 10 Molecule Types, 2024

Number of Drugs by Stage and Top 10 Molecule Types, 2024

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