Pompe Disease: Epidemiology Forecast to 2027

1 Table of Contents

1.1 List of Tables

1.2 List of Figures

2 Pompe Disease: Executive Summary

2.1 Related Reports

2.2 Upcoming Reports

3 Epidemiology

3.1 Disease Background

3.2 Risk Factors and Comorbidities

3.3 Global and Historical Trends

3.4 Forecast Methodology

3.4.1 Sources

3.4.2 Forecast Assumptions and Methods

3.4.3 Diagnosed Incident Cases of Pompe Disease – Based on International Registry Data

3.4.4 Diagnosed Incident Cases of Pompe Disease by Type – Based on International Registry Data

3.4.5 Diagnosed Incident Cases of LOPD by Severity – Based on International Registry Data

3.4.6 Diagnosed Incident Cases of IOPD by CRIM Status – Based on International Registry Data

3.4.7 Diagnosed Prevalent Cases of Pompe Disease – Based on International Registry Data

3.4.8 Diagnosed Prevalent Cases of Pompe Disease – Method-1

3.4.9 Diagnosed Prevalent Cases of Pompe Disease – Method-2

3.4.10 Forecast Adjusted for the Underestimation of International Registry Data

3.5 Epidemiological Forecast for Pompe Disease (2017–2027) – Based on International Registry Data

3.5.1 Diagnosed Incident Cases of Pompe Disease

3.5.2 Sex-Specific Diagnosed Incident Cases of Pompe Disease

3.5.3 Diagnosed Incident Cases of Pompe Disease by Type

3.5.4 Diagnosed Incident Cases of LOPD by Severity

3.5.5 Diagnosed Incident Cases of IOPD by CRIM Status

3.5.6 Diagnosed Prevalent Cases of Pompe Disease – Method-1

3.5.7 Diagnosed Prevalent Cases of Pompe Disease – Method-2

3.6 Epidemiological Forecast for Pompe Disease (2017–2027) – Adjusted for the Underestimation of International Registry Data

3.6.1 Diagnosed Incident Cases of Pompe Disease

3.6.2 Sex-Specific Diagnosed Incident Cases of Pompe Disease

3.6.3 Diagnosed Incident Cases of Pompe Disease by Type

3.6.4 Diagnosed Incident Cases of LOPD by Severity

3.6.5 Diagnosed Incident Cases of IOPD by CRIM Status

3.6.6 Diagnosed Prevalent Cases of Pompe Disease – Method-1

3.6.7 Diagnosed Prevalent Cases of Pompe Disease – Method-2

3.7 Discussion

3.7.1 Epidemiological Forecast Insight

3.7.2 Limitations of the Analysis

3.7.3 Strengths of the Analysis

4 Appendix

4.1 Bibliography

4.2 About the Authors

4.2.1 Epidemiologist

4.2.2 Reviewers

4.2.3 Global Director of Therapy Analysis and Epidemiology

4.2.4 Global Head and EVP of Healthcare Operations and Strategy

4.3 About GlobalData

4.4 Contact Us

4.5 Disclaimer

Table 1: Risk Factors for Pompe Disease

Figure 1: 8MM, Diagnosed Incident Cases of Pompe Disease, N, Both Sexes, All Ages, 2017 and 2027 (Forecast Adjusted for the Underestimation of International Registry Data)

Figure 2: 8MM, Diagnosed Prevalent Cases of Pompe Disease – Method-1, N, Both Sexes, All Ages, 2017 and 2027 (Forecast Adjusted for the Underestimation of International Registry Data)

Figure 3: 8MM, Diagnosed Prevalent Cases of Pompe Disease – Method-2, N, Both Sexes, All Ages, 2017 and 2027 (Forecast Adjusted for the Underestimation of International Registry Data))

Figure 4: 8MM, Sources Used to Forecast the Diagnosed Incident Cases of Pompe Disease

Figure 5: 8MM, Sources Used to Forecast the Diagnosed Prevalent Cases of Pompe Disease

Figure 6: 8MM, Sources Used to Forecast the Diagnosed Incident Cases of Pompe Disease by Type

Figure 7: 8MM, Sources Used to Forecast the Diagnosed Incident Cases of LOPD by Severity

Figure 8: 8MM, Sources Used to Forecast the Diagnosed Incident Cases of IOPD by CRIM Status

Figure 9: 8MM, Diagnosed Incident Cases of Pompe Disease, N, Both Sexes, All Ages, 2017 (Forecast Based on International Registry Data)

Figure 10: 8MM, Sex-Specific Diagnosed Incident Cases of Pompe Disease, N, All Ages, 2017 (Forecast Based on International Registry Data)

Figure 11: 8MM, Diagnosed Incident Cases of Pompe Disease by Type, N, Both Sexes, All Ages, 2017 (Forecast Based on International Registry Data)

Figure 12: 8MM, Diagnosed Incident Cases of LOPD by Severity, N, Both Sexes, All Ages, 2017 (Forecast Based on International Registry Data)

Figure 13: 8MM, Diagnosed Incident Cases of IOPD by CRIM Status, N, Both Sexes, All Ages, 2017 (Forecast Based on International Registry Data)

Figure 14: 8MM, Diagnosed Prevalent Cases of Pompe Disease – Method-1, N, Both Sexes, All Ages, 2017 (Forecast Based on International Registry Data)

Figure 15: 8MM, Diagnosed Prevalent Cases of Pompe Disease – Method-2, N, Both Sexes, All Ages, 2017 (Forecast Based on International Registry Data)

Figure 16: 8MM, Diagnosed Incident Cases of Pompe Disease, N, Both Sexes, All Ages, 2017 (Forecast Adjusted for the Underestimation of International Registry Data)

Figure 17: 8MM, Sex-Specific Diagnosed Incident Cases of Pompe Disease, N, All Ages, 2017 (Forecast Adjusted for the Underestimation of International Registry Data)

Figure 18: 8MM, Diagnosed Incident Cases of Pompe Disease by Type, N, Both Sexes, All Ages, 2017 (Forecast Adjusted for the Underestimation of International Registry Data)

Figure 19: 8MM, Diagnosed Incident Cases of LOPD by Severity, N, Both Sexes, All Ages, 2017 (Forecast Adjusted for the Underestimation of International Registry Data)

Figure 20: 8MM, Diagnosed Incident Cases of IOPD by CRIM Status, N, Both Sexes, All Ages, 2017 (Forecast Adjusted for the Underestimation of International Registry Data)

Figure 21: 8MM, Diagnosed Prevalent Cases of Pompe Disease – Method-1, N, Both Sexes, All Ages, 2017 (Forecast Adjusted for the Underestimation of International Registry Data)

Figure 22: 8MM, Diagnosed Prevalent Cases of Pompe Disease – Method-2, N, Both Sexes, All Ages, 2017 (Forecast Adjusted for the Underestimation of International Registry Data)