Aicardi-Goutieres Syndrome Marketed and Pipeline Drugs Assessment, Clinical Trials and Competitive Landscape

Pages: 52 Published: June 02, 2022 Report Code: GDHC065CL

Aicardi-Goutieres syndrome pipeline market report combines data from the Pharma Intelligence Center with in-house analyst expertise to provide a competitive assessment of the disease marketplace. Aicardi-Goutieres syndrome (AGS) is an inherited disease that mainly affects the brain, immune system, and the skin. Loss of white matter in the brain (leukodystrophy) and abnormal deposits of calcium (calcification) in the brain lead to early-onset severe brain dysfunction (encephalopathy) that usually results in severe intellectual and physical disability.

Which are the key countries for clinical trials in the Aicardi-Goutieres syndrome pipeline market?

The key countries for clinical trials in the Aicardi-Goutieres syndrome pipeline market are Japan, the US, the UK, and France. Japan has the highest share in the Aicardi-Goutieres syndrome pipeline market.

Aicardi-Goutieres syndrome pipeline market, by countries

Aicardi-Goutieres syndrome pipeline market, by countriesFor more country insights, download a free report sample

Which are the key development stages in the Aicardi-Goutieres syndrome pipeline market?

The key development stages in the Aicardi-Goutieres syndrome pipeline market are phase III, phase II, preclinical, and discovery. Preclinical stage has the highest share in the Aicardi-Goutieres syndrome pipeline market.

Aicardi-Goutieres syndrome pipeline market, by development stage

Aicardi-Goutieres syndrome pipeline market, by development stageFor more development stage insights, download a free report sample

Which is the key molecule type in the Aicardi-Goutieres syndrome pipeline market?

The key molecule type in the Aicardi-Goutieres syndrome pipeline market is small molecule.

Which are the key MoA in the Aicardi-Goutieres syndrome pipeline market?

The key MoA in the Aicardi-Goutieres syndrome pipeline market are enzyme inhibitor, and protein and peptide inhibitor. Enzyme inhibitor has the highest share in the Aicardi-Goutieres syndrome pipeline market.

Aicardi-Goutieres syndrome pipeline market, by MoA

Aicardi-Goutieres syndrome pipeline market, by MoAFor more MoA insights, download a free report sample

Which is the key RoA in the Aicardi-Goutieres syndrome pipeline market?

The key RoA in the Aicardi-Goutieres syndrome pipeline market is oral.

Which are the key sponsors in the Aicardi-Goutieres syndrome pipeline market?

The key sponsors in the Aicardi-Goutieres syndrome pipeline market are Eli Lilly and Co, Children’s Hospital of Philadelphia, Assistance Publique – Hopitaux de Paris, and University of Edinburgh.

Aicardi-Goutieres syndrome pipeline market, by sponsors

Aicardi-Goutieres syndrome pipeline market, by sponsorsTo know more about sponsors, download a free report sample

Market report overview

Key countries Japan, the US, the UK, and France
Key development stage Phase III, Phase II, Preclinical, and Discovery
Key molecule type Small Molecule
Key MoA Enzyme Inhibitor, and Protein and Peptide Inhibitor
Key RoA Oral
Key sponsors Eli Lilly and Co, Children’s Hospital of Philadelphia, Assistance Publique – Hopitaux de Paris, and University of Edinburgh

 Scope

GlobalData’s Aicardi-Goutieres Syndrome Marketed and Pipeline Drugs Assessment, Clinical Trials, Social Media and Competitive Landscape, 2022 Update combines data from the Pharma Intelligence Center with in-house analyst expertise to provide a competitive assessment of the disease marketplace.

Components of the report include:

  • Disease Landscape
  • Disease Overview
  • Epidemiology Overview
  • Treatment Overview
  • Marketed Products Assessment
  • Pipeline Assessment
  • Breakdown by Development Stage, Mechanism of Action, Molecule Type, Route of Administration
  • Late-stage Pipeline Drugs
  • Phase Transition Success Rate and Likelihood of Approval
  • Clinical Trials Assessment
  • Breakdown of Trials by Phase, Status, Sponsors and Geography
  • Enrolment Analytics, Site Analytics, Feasibility Analysis
  • Deals Landscape
  • Commercial Assessment
  • Key Market Players
  • Future Market Catalysts

Reasons to Buy

  • Develop and design your in-licensing and out-licensing strategies through a review of pipeline products and technologies, and by identifying the companies with the most robust pipeline.
  • Develop business strategies by understanding the trends shaping and driving the Aicardi-Goutieres Syndrome market.
  • Drive revenues by understanding the key trends, innovative products and technologies, market segments, and companies likely to impact the global Aicardi-Goutieres Syndrome market in the future.
  • Formulate effective sales and marketing strategies by understanding the competitive landscape and by analyzing the performance of various competitors.
  • Identify emerging players with potentially strong product portfolios and create effective counter-strategies to gain a competitive advantage.
  • Organize your sales and marketing efforts by identifying the market categories and segments that present maximum opportunities for consolidations, investments, and strategic partnerships.

Table of Contents

1 Preface

1.1 Contents

1.2 Report Scope

1.3 List of Tables and Figures

1.4 Abbreviations

2 Key Findings

3 Disease Landscape

3.1 Disease Overview

3.2 Epidemiology Overview

3.3 Treatment Overview

4 Marketed Drugs Assessment

5 Pipeline Drugs Assessment

5.1 Late-stage Pipeline Drugs

5.2 Overview by Development Stage

5.3 Overview by Molecule Type

5.4 Overview by Mechanism of Action

5.5 Overview by Route of Administration

5.6 Therapy Area and Indication-specific PTSR and LoA

6 Clinical Trials Assessment

6.1 Historical Overview

6.2 Overview by Phase

6.3 Overview by Status

6.4 Geographic Overview

6.5 Top 20 Sponsors with Breakdown by Phase

6.6 Top 20 Sponsors with Breakdown by Status

6.7 Enrollment Data

6.8 Top 20 countries for Trial Sites

6.9 Top 20 Sites Globally

6.10 Feasibility Analysis – Geographic Overview

6.11 Feasibility Analysis – Benchmark Models

7 Deals Landscape

8 Commercial Assessment

8.1 Key Market Players

9 Future Market Catalysts

10 Appendix

10.1 Methodology

10.2 Methodology – PTSR and LoA Analysis

10.3 About the Authors

10.4 Contact Us

10.5 Disclaimer

Frequently Asked Questions

Request a Free Sample
$3495

Can be used by individual purchaser only

$10485

Can be shared globally by unlimited users within the purchasing corporation e.g. all employees of a single company

Get in touch to find out about multi-purchase discounts

reportstore@globaldata.com
Tel +44 20 7947 2745

GDPR + CCPA Compliant

Personal and transaction information are kept safe from unauthorised use.

Recently Viewed Reports

Looking to stay on top of industry & market trends?

Sign up to receive regular alerts for our latest analysis and reports. No matter your industry focus, you can keep your finger on the pulse with our timely updates.