Paroxysmal Nocturnal Hemoglobinuria Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update
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The symptoms of Paroxysmal Nocturnal Hemoglobinuria include abdominal pain, back pain, dark urine, easy bruising or bleeding, headache, and shortness of breath. Its treatment includes surgery, chemotherapy, and radiation therapy.
Key Targets | Complement C5, Complement Factor D, Complement C3, Leukotriene B4, Complement Factor B, Mannan Binding Lectin Serine Protease 1, and Properdin |
Key Mechanisms of Action | Complement C5 Inhibitor, Complement Factor D Inhibitor, Complement C3 Inhibitor, Leukotriene B4 Inhibitor, Complement Factor B Inhibitor, Mannan Binding Lectin Serine Protease 1 Inhibitor, and Properdin Inhibitor |
Key Routes of Administration | Intravenous, Subcutaneous, Oral, Intravitreal, Inhalational, Ophthalmic, and Intravenous Drip |
Key Molecule Type | Monoclonal Antibody, Small Molecule, Antisense RNAi Oligonucleotide, Biologic, Enzyme, Fusion Protein, Gene Therapy, Recombinant Protein, Synthetic Peptide, and Peptide |
Major Companies | Alexion Pharmaceuticals Inc, NovelMed Therapeutics Inc, Akari Therapeutics Plc, Alnylam Pharmaceuticals Inc, Apellis Pharmaceuticals Inc, CANbridge Life Sciences Ltd, Novartis AG, Regeneron Pharmaceuticals Inc, Wuhan LL Science and Technology Development Co Ltd, and Aevitas Therapeutics Inc |
The Paroxysmal Nocturnal Hemoglobinuria pipeline market research report provides comprehensive information on the therapeutics under development for Paroxysmal Nocturnal Hemoglobinuria, complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA), and molecule type. The report also covers the descriptive pharmacological action of the therapeutics, its complete research and development history, and the latest news and press releases. Additionally, the report provides an overview of key players involved in therapeutic development for Paroxysmal Nocturnal Hemoglobinuria and features dormant and discontinued projects.
Paroxysmal Nocturnal Hemoglobinuria Pipeline Products Market - Key Targets
The key targets in the Paroxysmal Nocturnal Hemoglobinuria pipeline products market are Complement C5, Complement Factor D, Complement C3, Leukotriene B4, Complement Factor B, Mannan Binding Lectin Serine Protease 1, and Properdin.
Paroxysmal Nocturnal Hemoglobinuria Pipeline Products Market Analysis by Targets
For more target insights, download a free report sample
Paroxysmal Nocturnal Hemoglobinuria Pipeline Products Market - Key Mechanisms of Action
The key mechanisms of action in the Paroxysmal Nocturnal Hemoglobinuria pipeline products market are Complement C5 Inhibitor, Complement Factor D Inhibitor, Complement C3 Inhibitor, Leukotriene B4 Inhibitor, Complement Factor B Inhibitor, Mannan Binding Lectin Serine Protease 1 Inhibitor, and Properdin Inhibitor.
Paroxysmal Nocturnal Hemoglobinuria Pipeline Products Market Analysis by Mechanisms of Action
For more mechanisms of action insights, download a free report sample
Paroxysmal Nocturnal Hemoglobinuria Pipeline Products Market - Key Routes of Administration
The key routes of administration in the Paroxysmal Nocturnal Hemoglobinuria pipeline products market are intravenous, subcutaneous, oral, intravitreal, inhalational, ophthalmic, and intravenous drip.
Paroxysmal Nocturnal Hemoglobinuria Pipeline Products Market Analysis by Routes of Administration
For more routes of administration insights, download a free report sample
Paroxysmal Nocturnal Hemoglobinuria Pipeline Products Market - Key Molecule Types
The key molecule types in the Paroxysmal Nocturnal Hemoglobinuria pipeline products market are monoclonal antibody, small molecule, antisense RNAi oligonucleotide, biologic, enzyme, fusion protein, gene therapy, recombinant protein, synthetic peptide, and peptide.
Paroxysmal Nocturnal Hemoglobinuria Pipeline Products Market Analysis by Molecule Types
For more molecule type insights, download a free report sample
Competitive Landscape
Some of the major companies in the Paroxysmal Nocturnal Hemoglobinuria pipeline products market are Alexion Pharmaceuticals Inc, NovelMed Therapeutics Inc, Akari Therapeutics Plc, Alnylam Pharmaceuticals Inc, Apellis Pharmaceuticals Inc, CANbridge Life Sciences Ltd, Novartis AG, Regeneron Pharmaceuticals Inc, Wuhan LL Science and Technology Development Co Ltd, and Aevitas Therapeutics Inc.
Paroxysmal Nocturnal Hemoglobinuria Pipeline Products Market Analysis by Companies
To know more about major companies, download a free report sample
Scope
- The pipeline guide provides a snapshot of the global therapeutic landscape of Paroxysmal Nocturnal Hemoglobinuria (Hematological Disorders).
- The pipeline guide reviews pipeline therapeutics for Paroxysmal Nocturnal Hemoglobinuria (Hematological Disorders) by companies and universities/research institutes based on information derived from company and industry-specific sources.
- The pipeline guide covers pipeline products based on several stages of development ranging from pre-registration till discovery and undisclosed stages.
- The pipeline guide features descriptive drug profiles for the pipeline products which comprise, product description, descriptive licensing and collaboration details, R&D brief, MoA & other developmental activities.
- The pipeline guide reviews key companies involved in Paroxysmal Nocturnal Hemoglobinuria (Hematological Disorders) therapeutics and enlists all their major and minor projects.
- The pipeline guide evaluates Paroxysmal Nocturnal Hemoglobinuria (Hematological Disorders) therapeutics based on mechanism of action (MoA), drug target, route of administration (RoA), and molecule type.
- The pipeline guide encapsulates all the dormant and discontinued pipeline projects.
- The pipeline guide reviews the latest news related to pipeline therapeutics for Paroxysmal Nocturnal Hemoglobinuria (Hematological Disorders)
Reasons to Buy
- Procure strategically important competitor information, analysis, and insights to formulate effective R&D strategies.
- Recognize emerging players with potentially strong product portfolios and create effective counter-strategies to gain competitive advantage.
- Find and recognize significant and varied types of therapeutics under development for Paroxysmal Nocturnal Hemoglobinuria (Hematological Disorders).
- Classify potential new clients or partners in the target demographic.
- Develop tactical initiatives by understanding the focus areas of leading companies.
- Plan mergers and acquisitions meritoriously by identifying key players and their most promising pipeline therapeutics.
- Formulate corrective measures for pipeline projects by understanding Paroxysmal Nocturnal Hemoglobinuria (Hematological Disorders) pipeline depth and focus of Indication therapeutics.
- Develop and design in-licensing and out-licensing strategies by identifying prospective partners with the most attractive projects to enhance and expand business potential and scope.
- Adjust the therapeutic portfolio by recognizing discontinued projects and understand from the know-how what drove them from the pipeline.
Akari Therapeutics Plc
Alexion Pharmaceuticals Inc
Alnylam Pharmaceuticals Inc
Amgen Inc
Amyndas Pharmaceuticals LLC
Apellis Pharmaceuticals Inc
Arrowhead Pharmaceuticals Inc
Attune Pharmaceuticals
Biocad
BioCryst Pharmaceuticals Inc
CANbridge Life Sciences Ltd
Chugai Pharmaceutical Co Ltd
Homology Medicines Inc
ImmunAbs Inc
ISU ABXIS Co Ltd
Kira Pharmaceuticals
Novartis AG
NovelMed Therapeutics Inc
Omeros Corp
Prestige BioPharma Ltd
Ra Pharmaceuticals Inc
Rallybio Corp
Regeneron Pharmaceuticals Inc
Samsung Bioepis Co Ltd
Shanghai ComGen Biopharmaceutical Co Ltd
Shanghai Meiyue Biotechnology Development Co Ltd
Tasly Biopharmaceuticals Co Ltd
Turgut Ilaclari AS
Wuhan LL Science and Technology Development Co Ltd
Zydus Lifesciences Ltd
Table of Contents
Frequently asked questions
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What are the key targets in the Paroxysmal Nocturnal Hemoglobinuria products market?
The key targets in the Paroxysmal Nocturnal Hemoglobinuria pipeline products market are Complement C5, Complement Factor D, Complement C3, Leukotriene B4, Complement Factor B, Mannan Binding Lectin Serine Protease 1, and Properdin.
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What are the key mechanisms of action in the Paroxysmal Nocturnal Hemoglobinuria pipeline products market?
The key mechanisms of action in the Paroxysmal Nocturnal Hemoglobinuria pipeline products market are Complement C5 Inhibitor, Complement Factor D Inhibitor, Complement C3 Inhibitor, Leukotriene B4 Inhibitor, Complement Factor B Inhibitor, Mannan Binding Lectin Serine Protease 1 Inhibitor, and Properdin Inhibitor.
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What are the key routes of administration in the Paroxysmal Nocturnal Hemoglobinuria pipeline products market?
The key routes of administration in the Paroxysmal Nocturnal Hemoglobinuria pipeline products market are intravenous, subcutaneous, oral, intravitreal, inhalational, ophthalmic, and intravenous drip.
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What are the key molecule types in the Paroxysmal Nocturnal Hemoglobinuria pipeline products market?
The key molecule types in the Paroxysmal Nocturnal Hemoglobinuria pipeline products market are monoclonal antibody, small molecule, antisense RNAi oligonucleotide, biologic, enzyme, fusion protein, gene therapy, recombinant protein, synthetic peptide, and peptide.
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Which are the major companies in the Paroxysmal Nocturnal Hemoglobinuria pipeline products market?
Some of the major companies in the Paroxysmal Nocturnal Hemoglobinuria pipeline products market are Alexion Pharmaceuticals Inc, NovelMed Therapeutics Inc, Akari Therapeutics Plc, Alnylam Pharmaceuticals Inc, Apellis Pharmaceuticals Inc, CANbridge Life Sciences Ltd, Novartis AG, Regeneron Pharmaceuticals Inc, Wuhan LL Science and Technology Development Co Ltd, and Aevitas Therapeutics Inc.
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