Abeona Therapeutics Inc - Company Profile
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Business Description
Abeona Therapeutics Inc. is a clinical-stage biopharmaceutical company focused on developing cell and gene therapies for severe, life-threatening conditions. Its pipeline includes programs for recessive dystrophic epidermolysis bullosa (RDEB) and several inherited eye diseases using adeno-associated virus (AAV) gene therapy approaches.
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R&D Overview
Abeona’s R&D is focused on advancing and commercializing cell and gene therapy programs, including the development of ZEVASKYN and ABO-504. The company is leveraging its expertise in research and development to introduce efficacious and safe therapeutics aimed at transforming the standard of care in devastating diseases. The company is also actively seeking U.S. and international patent protection for various technologies, including AAV capsids and AAV-based biological products, and is involved in strategic partnerships and collaborations with academic institutions and industry partners to accelerate research and development. Its R&D unit is responsible for developing cell and gene therapy programs, including the design and implementation of novel AAV vector strategies, conducting preclinical and clinical studies, and ensuring compliance with regulatory requirements. The unit also focuses on securing intellectual property rights and collaborating with external partners to enhance research and development efforts. In FY2025, the company spent US$26.8 million on its R&D activities, which grew 21.9% YoY.
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